共 44 条
- [41] Bioinformatic Identification and Large-Scale In Vitro and In Vivo Characterization of Human-Derived Novel AAV2 and AAV2/3 Capsid Variants Reveals Vectors with New Biological FunctionsMOLECULAR THERAPY, 2017, 25 (05) : 231 - 231Luo, Li论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAXu, Guangchao论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USATai, Phillip W. L.论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Microbiol & Physiol Syst, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAQin, Wanru论文数: 0 引用数: 0 h-index: 0机构: Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAXiao, Yuanyuan论文数: 0 引用数: 0 h-index: 0机构: Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAWang, Chunmei论文数: 0 引用数: 0 h-index: 0机构: Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAMa, Hong论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAHe, Ran论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USASu, Qin论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAFong, Kaiyuen论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAGong, Shoufang论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAWei, Yuquan论文数: 0 引用数: 0 h-index: 0机构: Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USAGao, Guangping论文数: 0 引用数: 0 h-index: 0机构: Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA Sichuan Univ, West China Hosp, State Key Lab Biotherapy, Chengdu, Peoples R China Univ Massachusetts, Sch Med, Microbiol & Physiol Syst, Worcester, MA USA Univ Massachusetts, Sch Med, Viral Vector Core, Worcester, MA USA Univ Massachusetts, Sch Med, Horae Gene Therapy Ctr, Worcester, MA USA
- [42] Stepwise Evolution of the AAV5-Derived Capsid VCAP-100 Identifies Novel Variants with Improved CNS Transduction and Liver Detargeting Following Systemic InjectionMOLECULAR THERAPY, 2023, 31 (04) : 238 - 239Maura, Damien论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAYu, Jennifer C.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAChild, Matthew论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAKaur, Roop论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAThorpe, Zachary论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USARen, Xiaoqin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAGebremedhin, Netsanet论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USALi, Jiangyu论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USALiu, Jiachen论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAFiore, Timothy论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAKavanagh, Dillon论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAKubiak, Alexander论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAGrant, Kyle论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USASayed-Zahid, Ambreen论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAMoyer, Tyler论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAGraham, Kristin P.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAKutchin, Alexander论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAYao, Johnny论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USACarter, Todd A.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USANonnenmacher, Mathieu E.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA
- [43] Directed Evolution of AAV9 Peptide Display Libraries Identifies a Family of Cross-Species Variants with Enhanced Brain Tropism in Non-Human Primates and Mice Following Systemic AdministrationMOLECULAR THERAPY, 2022, 30 (04) : 556 - 557Moyer, Tyler论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USALi, Jiangyu论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USALaks, Dan R.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAChild, Matthew A.论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USATyson, Katherine论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAKaur, Rupinderjit论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USARen, Xiao-Qin论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USASayed-Zahid, Ambreen论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAGrannon, Michael论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAChung, Charlotte Hiu-Yan论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAPande, Nilesh论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAThompson, Jeff论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAWang, Wei论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAHasson, Samuel论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USAHefferan, Michael论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USANonnenmacher, Mathieu论文数: 0 引用数: 0 h-index: 0机构: Voyager Therapeut, Cambridge, MA USA Voyager Therapeut, Cambridge, MA USA
- [44] CB 2679d-GT - A Novel Human Factor IX Variant Shows Enhanced Activity After Delivery Into Hemophilic Mice Using an AAV Capsid with High Liver TransductionMOLECULAR THERAPY, 2020, 28 (04) : 172 - 173Pekrun, Katja论文数: 0 引用数: 0 h-index: 0机构: Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USABlouse, Grant E.论文数: 0 引用数: 0 h-index: 0机构: Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USAZhang, Feijie论文数: 0 引用数: 0 h-index: 0机构: Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USALe Moan, Natacha论文数: 0 引用数: 0 h-index: 0机构: Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USAKnudsen, Tom论文数: 0 引用数: 0 h-index: 0机构: Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USALandau, Jeff论文数: 0 引用数: 0 h-index: 0机构: Catalyst Biosci, San Francisco, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USAKay, Mark A.论文数: 0 引用数: 0 h-index: 0机构: Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA Stanford Med Sch, Dept Pediat & Genet, Stanford, CA USA