Robust in vivo gene editing in mouse hepatocytes with systemic lipid nanoparticle delivery of CRISPR/Cas9 components

被引：0

作者：

Finn, J. D. ^{[1
]}

Patel, M. ^{[1
]}

Smith, A. Rhoden ^{[1
]}

Shaw, L. ^{[1
]}

Youniss, M. ^{[1
]}

Ciullo, C. ^{[1
]}

van Heteren, J. ^{[1
]}

Lescarbeau, R. ^{[1
]}

Seitzer, J. ^{[1
]}

Growe, J. ^{[1
]}

Dombrowski, C. ^{[1
]}

Strapps, W. R. ^{[1
]}

Barnes, T. M. ^{[1
]}

Morrissey, D. V. ^{[1
]}

机构：

[1] Intellia Therapeut, Cambridge, MA USA

来源：

HUMAN GENE THERAPY | 2016年 / 27卷 / 11期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P280

引用

页码：A131 / A131

页数：1

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