Robust in vivo gene editing in mouse hepatocytes with systemic lipid nanoparticle delivery of CRISPR/Cas9 components

被引：0
|
作者：
Finn, J. D. [1 ]
Patel, M. [1 ]
Smith, A. Rhoden [1 ]
Shaw, L. [1 ]
Youniss, M. [1 ]
Ciullo, C. [1 ]
van Heteren, J. [1 ]
Lescarbeau, R. [1 ]
Seitzer, J. [1 ]
Growe, J. [1 ]
Dombrowski, C. [1 ]
Strapps, W. R. [1 ]
Barnes, T. M. [1 ]
Morrissey, D. V. [1 ]
机构：
[1] Intellia Therapeut, Cambridge, MA USA
来源：
HUMAN GENE THERAPY | 2016年 / 27卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P280
引用
收藏
页码：A131 / A131
页数：1
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