Spliceosome mediated RNA trans-splicing (SMaRT) is a novel method to treat autosomal dominant diseases

被引：0
|
作者：
Wally, V
Klausegger, A.
Koller, U.
Lochmueller, H.
Krause, S.
Wiche, G.
Mitchell, L. G.
Hintner, H.
Bauer, J. W.
机构：
[1] Univ Munich, Dept Neurol, Friedrich Baur Inst, D-8000 Munich, Germany
[2] Univ Vienna, Max F Perutz Labs, Inst Biochem & Mol Biol, A-1010 Vienna, Austria
[3] Intronn Inc, Gaithersburg, MD USA
来源：
JOURNAL OF INVESTIGATIVE DERMATOLOGY | 2006年 / 126卷
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D O I：
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中图分类号：
R75 [皮肤病学与性病学];
学科分类号：
100206 ;
摘要：
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页码：32 / 32
页数：1
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