Therapy of the dynamin 2-linked centronuclear myopathy by naRNA repair using Spliceosome-Mediated RNA Trans-splicing (SMarT) strategy

被引：0
|
作者：
Trochet, D.
Prudhon, B.
Jollet, A.
Bitoun, M.
机构：
[1] Univ Paris 06, Res Ctr Myol, Paris, France
[2] CNRS ERR 3617, INSERM UMRS 974, Inst Myol, Paris, France
来源：
NEUROMUSCULAR DISORDERS | 2014年 / 24卷 / 9-10期
关键词：
D O I：
10.1016/j.nmd.2014.06.059
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
G.P.45
引用
收藏
页码：808 / 808
页数：1
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