AAV Vector-Mediated Iduronidase Gene Delivery in a Murine Model of Mucopolysaccharidosis Type I: Comparing Different Routes of Delivery to the CNS

被引：0
|
作者：
Belur, Lalitha [1 ]
Nan, Zhenhong [1 ]
Podetz-Pedersen, Kelly M. [1 ]
Fairbanks, Carolyn A. [1 ]
Hanson, Leah R. [2 ]
Frey, William H. [2 ]
Kozarsky, Karen [3 ]
Low, Walter C. [1 ]
McIvor, R. Scott [1 ]
机构：
[1] Univ Minnesota, Minneapolis, MN USA
[2] Reg Hosp, Alzheimers Res Ctr, St Paul, MN USA
[3] ReGenX Biosci, Washington, DC USA
来源：
MOLECULAR THERAPY | 2013年 / 21卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
364
引用
收藏
页码：S140 / S140
页数：1
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