Lentiviral Vector-Mediated Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIIA (MPSIIIA)

被引：0
|
作者：
Langford-Smith, A. W. W. [1 ]
Wilkinson, F. L. [1 ]
Langford-Smith, K. J. [1 ]
Bennett, W. [1 ]
Howe, S. [2 ]
Thrasher, A. [2 ]
Hemsley, K. [3 ]
Hopwood, J. [6 ]
Wraith, J. E. [4 ]
Wynn, R. F. [5 ]
Bigger, B. W. [1 ]
机构：
[1] Univ Manchester, MPS Stem Cell Res Grp, Clin Lab Sci, Manchester, Lancs, England
[2] UCL, Ctr Immunodeficiency, Mol Immunol Unit, Inst Child Hlth, London, England
[3] Adelaide Womens & Childrens Hosp, LDRU, Adelaide, SA, Australia
[4] St Marys Hosp, Manchester M13 0JH, Lancs, England
[5] Royal Manchester Childrens Hosp, Blood & Marrow Transplant Unit, Manchester M27 1HA, Lancs, England
[6] Adelaide Womens & Childrens Hosp, DRU, Adelaide, SA, Australia
来源：
HUMAN GENE THERAPY | 2010年 / 21卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：502 / 503
页数：2
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