Novartis Confirms Deaths of Two Patients Treated with Gene Therapy Zolgensma

被引:37
|
作者
Philippidis, Alex [1 ]
机构
[1] Mary Ann Liebert Inc, New Rochelle, NY 10801 USA
关键词
D O I
10.1089/hum.2022.29216.bfs
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
[No abstract available]
引用
收藏
页码:842 / 844
页数:3
相关论文
共 50 条
  • [41] A comprehensive safety analysis confirms rhabdomyolysis as an uncommon adverse reaction in patients treated with trabectedin
    Grosso, Federica
    D'Incalci, Maurizio
    Cartoafa, Mirela
    Nieto, Antonio
    Fernandez-Teruel, Carlos
    Alfaro, Vicente
    Lardelli, Pilar
    Roy, Elena
    Gomez, Javier
    Kahatt, Carmen
    Soto-Matos, Arturo
    Judson, Ian
    CANCER CHEMOTHERAPY AND PHARMACOLOGY, 2012, 69 (06) : 1557 - 1565
  • [42] Serial Angiography Depicts and Confirms the Neo-Angiogenesis Destroy in PRRT Treated Patients
    Karfis, I.
    Chatzioannou, A.
    Chalioti, M.
    Papamichail, D.
    Theodorakopoulos, V.
    Theofilatou, V.
    Gouliamos, A.
    Stavraka, A.
    Limouris, G. S.
    EUROPEAN JOURNAL OF NUCLEAR MEDICINE AND MOLECULAR IMAGING, 2012, 39 : S407 - S407
  • [43] A comprehensive safety analysis confirms rhabdomyolysis as an uncommon adverse reaction in patients treated with trabectedin
    Federica Grosso
    Maurizio D’Incalci
    Mirela Cartoafa
    Antonio Nieto
    Carlos Fernández-Teruel
    Vicente Alfaro
    Pilar Lardelli
    Elena Roy
    Javier Gómez
    Carmen Kahatt
    Arturo Soto-Matos
    Ian Judson
    Cancer Chemotherapy and Pharmacology, 2012, 69 : 1557 - 1565
  • [44] ANALYSIS OF POINT MUTATIONS IN THE HPRT GENE OF CANCER-PATIENTS TREATED WITH RADIOIMMUNOGLOBULIN THERAPY
    SKANDALIS, A
    CURRY, J
    ONEILL, JP
    NICKLAS, JA
    ALBERTINI, RJ
    GLICKMAN, BW
    ENVIRONMENTAL AND MOLECULAR MUTAGENESIS, 1995, 26 (03) : 213 - 217
  • [45] Hematopoietic stem cell behavior in gene therapy treated beta-thalassemia patients
    Lidonnici, M. R.
    Mende, N.
    Chianella, G.
    Tiboni, F.
    Barcella, M.
    Scaramuzza, S.
    Rossi, C.
    Merelli, I.
    Ciceri, F.
    Aiuti, A.
    Marktel, S.
    Laurenti, E.
    Ferrari, G.
    HUMAN GENE THERAPY, 2022, 33 (23-24) : A66 - A66
  • [46] Recombinant Adeno-Associated Virus Gene Therapy in Light of Luxturna (and Zolgensma and Glybera): Where Are We, and How Did We Get Here?
    Keeler, Allison M.
    Flotte, Terence R.
    ANNUAL REVIEW OF VIROLOGY, VOL 6, 2019, 2019, 6 : 601 - 621
  • [47] Can Alport syndrome be treated by gene therapy?
    Tryggvason, K
    Heikkila, P
    Pettersson, E
    Tibell, A
    Thorner, P
    KIDNEY INTERNATIONAL, 1997, 51 (05) : 1493 - 1499
  • [48] The Nursing Management of WAS Children Treated With Gene Therapy
    Casiraghi, M.
    Tresoldi, R.
    Ciceri, A.
    Milanovic, M.
    Moser, C.
    Cicalese, M. P.
    Ferrua, F.
    Roncarolo, M. G.
    Aiuti, A.
    Soliman, C.
    JOURNAL OF CLINICAL IMMUNOLOGY, 2014, 34 : S508 - S509
  • [49] Generation of AAV9 Gene Therapy Capsid Variants Capable of Evading Neutralizing anti-AAV9 Antibodies derived from Patients Post-Zolgensma® Treatment
    Potts, Lindsay
    Hsi, Jane
    Mietzsch, Mario
    Zachary, Jon
    Nelson, Austin
    Logan, Grant
    Alexander, Ian
    Huiskonen, Juha
    Mckenna, Robert
    JOURNAL OF BIOLOGICAL CHEMISTRY, 2024, 300 (03) : S43 - S43
  • [50] Therapy-related acute leukemia in two patients with multiple sclerosis treated with Mitoxantrone
    Colovic, Natasa
    Suvajdzic, Nada
    Kurtovic, Nada Kraguljac
    Djordjevic, Vesna
    Fekete, Marija Dencic
    Drulovic, Jelena
    Vidovic, Ana
    Tomin, Dragica
    BIOMEDICINE & PHARMACOTHERAPY, 2012, 66 (03) : 173 - 174