共 50 条
- [21] Haemophilia gene therapy: experiences and lessons from treated patientsOrphanet Journal of Rare Diseases, 17Cedric Hermans论文数: 0 引用数: 0 h-index: 0机构: Cliniques universitaires Saint-Luc,Division of Adult Hematology, Haemostasis and Thrombosis Unit
- [22] Gene Therapy for Spinal Muscular Atrophy (SMA): A Review of Current Challenges and Safety Considerations for Onasemnogene Abeparvovec (Zolgensma)CUREUS JOURNAL OF MEDICAL SCIENCE, 2023, 15 (03)Ogbonmide, Tolu论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Coll Med, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentRathore, Rajni论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Pharmacol & Therapeut, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentRangrej, Shahid B.论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Anat Res, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentHutchinson, Stedrea论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Pharmacol, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentLewis, Marcia论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Coll Med, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentOjilere, Stephenie论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Coll Med, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentCarvalho, Victoria论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Coll Med, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St VincentKelly, Irenaissia论文数: 0 引用数: 0 h-index: 0机构: St James Sch Med, Neurol, Arnos Vale, St Vincent St James Sch Med, Coll Med, Arnos Vale, St Vincent
- [23] Therapy-related cafe coronary deaths - Two case reports of rare asphyxial deaths in patients under supervised careAMERICAN JOURNAL OF FORENSIC MEDICINE AND PATHOLOGY, 2002, 23 (02): : 149 - 154Hunsaker, DM论文数: 0 引用数: 0 h-index: 0机构: Univ Louisville, Sch Med, Off Chief Med Examiner, Urban Govt Ctr, Louisville, KY 40204 USA Univ Louisville, Sch Med, Off Chief Med Examiner, Urban Govt Ctr, Louisville, KY 40204 USAHunsaker, JC论文数: 0 引用数: 0 h-index: 0机构: Univ Louisville, Sch Med, Off Chief Med Examiner, Urban Govt Ctr, Louisville, KY 40204 USA Univ Louisville, Sch Med, Off Chief Med Examiner, Urban Govt Ctr, Louisville, KY 40204 USA
- [24] High-dose AAV gene therapy deathsNATURE BIOTECHNOLOGY, 2020, 38 (08) : 910 - 910不详论文数: 0 引用数: 0 h-index: 0
- [26] Re: "Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy" by Wilson and FlotteHUMAN GENE THERAPY, 2020, 31 (15-16) : 787 - 787Shieh, Perry B.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Los Angeles, Sch Med, Los Angeles, CA USA Univ Calif Los Angeles, Sch Med, Los Angeles, CA USABonnemann, Carsten G.论文数: 0 引用数: 0 h-index: 0机构: NINDS, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA Univ Calif Los Angeles, Sch Med, Los Angeles, CA USAMueller-Felber, Wolfgang论文数: 0 引用数: 0 h-index: 0机构: Klinikum Univ Munchen, Munich, Germany Univ Calif Los Angeles, Sch Med, Los Angeles, CA USABlaschek, Astrid论文数: 0 引用数: 0 h-index: 0机构: Klinikum Univ Munchen, Munich, Germany Univ Calif Los Angeles, Sch Med, Los Angeles, CA USADowling, James J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Sick Children, Toronto, ON, Canada Univ Calif Los Angeles, Sch Med, Los Angeles, CA USAKuntz, Nancy L.论文数: 0 引用数: 0 h-index: 0机构: Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL 60611 USA Univ Calif Los Angeles, Sch Med, Los Angeles, CA USASeferian, Andreea M.论文数: 0 引用数: 0 h-index: 0机构: Hop La Pitie Salpetriere, Inst Myol, Paris, France Univ Calif Los Angeles, Sch Med, Los Angeles, CA USA
- [27] Outcomes in Two Japanese Adenosine Deaminase-Deficiency Patients Treated by Stem Cell Gene Therapy with No Cytoreductive ConditioningJournal of Clinical Immunology, 2015, 35 : 384 - 398Makoto Otsu论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceMasafumi Yamada论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceSatoru Nakajima论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceMiyuki Kida论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceYoshihiro Maeyama论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceNorikazu Hatano论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceNariaki Toita论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceShunichiro Takezaki论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceYuka Okura论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceRyoji Kobayashi论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceYoshinori Matsumoto论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceOsamu Tatsuzawa论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceFumiko Tsuchida论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceShunichi Kato论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceMasanari Kitagawa论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceJunichi Mineno论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceMichael S. Hershfield论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical SciencePawan Bali论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceFabio Candotti论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceMasafumi Onodera论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceNobuaki Kawamura论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceYukio Sakiyama论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical ScienceTadashi Ariga论文数: 0 引用数: 0 h-index: 0机构: University of Tokyo,Center for Stem Cell Biology and Regenerative Medicine, Institute of Medical Science
- [28] Outcomes in Two Japanese Adenosine Deaminase-Deficiency Patients Treated by Stem Cell Gene Therapy with No Cytoreductive ConditioningJOURNAL OF CLINICAL IMMUNOLOGY, 2015, 35 (04) : 384 - 398Otsu, Makoto论文数: 0 引用数: 0 h-index: 0机构: Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, Japan Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanYamada, Masafumi论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanNakajima, Satoru论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanKida, Miyuki论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanMaeyama, Yoshihiro论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanHatano, Norikazu论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanToita, Nariaki论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanTakezaki, Shunichiro论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanOkura, Yuka论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanKobayashi, Ryoji论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanMatsumoto, Yoshinori论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanTatsuzawa, Osamu论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Child Hlth & Dev, Dept Human Genet, Tokyo, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanTsuchida, Fumiko论文数: 0 引用数: 0 h-index: 0机构: Tokai Univ, Sch Med, Dept Cell Transplantat & Regenerat Med, Hiratsuka, Kanagawa 25912, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanKato, Shunichi论文数: 0 引用数: 0 h-index: 0机构: Tokai Univ, Sch Med, Dept Cell Transplantat & Regenerat Med, Hiratsuka, Kanagawa 25912, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanKitagawa, Masanari论文数: 0 引用数: 0 h-index: 0机构: Takara Bio, Shiga, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanMineno, Junichi论文数: 0 引用数: 0 h-index: 0机构: Takara Bio, Shiga, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanHershfield, Michael S.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Biochem, Durham, NC USA Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanBali, Pawan论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Sch Med, Dept Biochem, Durham, NC USA Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanCandotti, Fabio论文数: 0 引用数: 0 h-index: 0机构: NHGRI, Genet & Mol Biol Branch, NIH, Bethesda, MD 20892 USA Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanOnodera, Masafumi论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Child Hlth & Dev, Dept Human Genet, Tokyo, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanKawamura, Nobuaki论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanSakiyama, Yukio论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, JapanAriga, Tadashi论文数: 0 引用数: 0 h-index: 0机构: Hokkaido Univ, Grad Sch Med, Dept Pediat, Kita Ku, Sapporo, Hokkaido 0608638, Japan Hokkaido Univ, Grad Sch Med, Res Grp Human Gene Therapy, Sapporo, Hokkaido 0608638, Japan Univ Tokyo, Inst Med Sci, Ctr Stem Cell Biol & Regenerat Med, Tokyo, Japan
- [29] Reconstitution of Hematopoiesis in Patients Treated with Gene Therapy for Beta-ThalassemiaMOLECULAR THERAPY, 2018, 26 (05) : 3 - 3Lidonnici, Maria Rosa论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy SR TIGET, Milan, ItalyScaramuzza, Samantha论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy SR TIGET, Milan, ItalyRossi, Claudia论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy SR TIGET, Milan, ItalyTiboni, Francesca论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy SR TIGET, Milan, ItalyCiceri, Fabio论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Haematol & BMT Unit, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy SR TIGET, Milan, ItalyAiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy IRCCS San Raffaele Sci Inst, Pediat Immunohematol, Milan, Italy SR TIGET, Milan, ItalyMarktel, Sarah论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy IRCCS San Raffaele Sci Inst, Haematol & BMT Unit, Milan, Italy SR TIGET, Milan, ItalyFerrari, Giuliana论文数: 0 引用数: 0 h-index: 0机构: SR TIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy SR TIGET, Milan, Italy
- [30] UPDATE ON THE FIRST PATIENTS WITH SEVERE HEMOGLOBINOPATHIES TREATED WITH LENTIGLOBIN GENE THERAPYHAEMATOLOGICA, 2017, 102 : 248 - 248Ribeil, J. -A.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceHacein-Bey-Abina, S.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FrancePayen, E.论文数: 0 引用数: 0 h-index: 0机构: CEA, Inst Emerging Dis & Innovat Therapies iMETI, Fontenay Aux Roses, France Univ Paris Sud, Fontenay Aux Roses, France Hop Necker Enfants Malad, Paris, FranceMagrin, E.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceMagnani, A.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceSemeraro, M.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Paris, France Hop Necker Enfants Malad, Paris, FranceCaccavelli, L.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceTouzot, F.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceLefrere, F.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceSuarez, F.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceHermine, O.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceBrousse, V.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FrancePoirot, C.论文数: 0 引用数: 0 h-index: 0机构: Hop St Louis, Paris, France Hop Necker Enfants Malad, Paris, FranceMoshous, D.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceBourget, P.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceEl-Nemer, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Diderot, Paris, France Hop Necker Enfants Malad, Paris, FranceBartolucci, P.论文数: 0 引用数: 0 h-index: 0机构: Hop Henri Mondor, Paris, France Hop Necker Enfants Malad, Paris, FranceWeber, L.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris 05, Paris, France Hop Necker Enfants Malad, Paris, FrancePuy, H.论文数: 0 引用数: 0 h-index: 0机构: Hop Henri Mondor, Paris, France Hop Necker Enfants Malad, Paris, FranceMeritet, J. -F.论文数: 0 引用数: 0 h-index: 0机构: Hop Cochin St Vincent Paul, Paris, France Hop Necker Enfants Malad, Paris, FranceGrevent, D.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceBuezard, Y.论文数: 0 引用数: 0 h-index: 0机构: CEA, Inst Emerging Dis & Innovat Therapies iMETI, Fontenay Aux Roses, France Univ Paris Sud, Fontenay Aux Roses, France Hop Necker Enfants Malad, Paris, FranceChretien, S.论文数: 0 引用数: 0 h-index: 0机构: CEA, Inst Emerging Dis & Innovat Therapies iMETI, Fontenay Aux Roses, France Univ Paris Sud, Fontenay Aux Roses, France Hop Necker Enfants Malad, Paris, France论文数: 引用数: h-index:机构:Asmal, M.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio, Cambridge, MA USA Hop Necker Enfants Malad, Paris, FranceSandler, L.论文数: 0 引用数: 0 h-index: 0机构: Bluebird Bio, Cambridge, MA USA Hop Necker Enfants Malad, Paris, Francede Montalembert, M.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, FranceBlanche, S.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, France论文数: 引用数: h-index:机构:Cavazzana, M.论文数: 0 引用数: 0 h-index: 0机构: Hop Necker Enfants Malad, Paris, France Hop Necker Enfants Malad, Paris, France