Efficient Targeted Gene Modification in Primary Human Hematopoietic Cells Using Co-Delivery of Nuclease mRNA and AAV Donors

被引：0
|
作者：
Ibarra, Guillermo S. Romano [1 ,2 ]
Curinga, Gabrielle [1 ,2 ]
Sather, Blythe D. [1 ,2 ]
Sommer, Karen M. [1 ,2 ]
Hale, Malika [1 ,2 ]
Khan, Iram [1 ,2 ]
Singh, Swati [1 ,2 ]
Song, Youmei [1 ,2 ]
Gwiazda, Kamila [1 ,2 ]
Sahni, Jaya [1 ,2 ]
Khim, Socheath [1 ,2 ]
Astrakhan, Alexander [3 ]
Wagner, Thor [1 ,2 ,4 ]
Scharenberg, Andrew M. [1 ,2 ,4 ]
Rawlings, David J. [1 ,2 ,4 ]
机构：
[1] Seattle Childrens Res Inst, Ctr Immun & Immunotherapies, Seattle, WA USA
[2] Seattle Childrens Res Inst, Program Cell & Gene Therapy, Seattle, WA USA
[3] Bluebird Bio, Bluebird Bio Seattle, Seattle, WA USA
[4] Univ Washington, Sch Med, Seattle, WA USA
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
685
引用
收藏
页码：S273 / S273
页数：1
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