Efficient Targeted Gene Modification in Primary Human Hematopoietic Cells Using Co-Delivery of Nuclease mRNA and AAV Donors

被引：0

作者：

Ibarra, Guillermo S. Romano ^{[1
,2
]}

Curinga, Gabrielle ^{[1
,2
]}

Sather, Blythe D. ^{[1
,2
]}

Sommer, Karen M. ^{[1
,2
]}

Hale, Malika ^{[1
,2
]}

Khan, Iram ^{[1
,2
]}

Singh, Swati ^{[1
,2
]}

Song, Youmei ^{[1
,2
]}

Gwiazda, Kamila ^{[1
,2
]}

Sahni, Jaya ^{[1
,2
]}

Khim, Socheath ^{[1
,2
]}

Astrakhan, Alexander ^{[3
]}

Wagner, Thor ^{[1
,2
,4
]}

Scharenberg, Andrew M. ^{[1
,2
,4
]}

Rawlings, David J. ^{[1
,2
,4
]}

机构：

[1] Seattle Childrens Res Inst, Ctr Immun & Immunotherapies, Seattle, WA USA

[2] Seattle Childrens Res Inst, Program Cell & Gene Therapy, Seattle, WA USA

[3] Bluebird Bio, Bluebird Bio Seattle, Seattle, WA USA

[4] Univ Washington, Sch Med, Seattle, WA USA

来源：

MOLECULAR THERAPY | 2015年 / 23卷

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

685

引用

页码：S273 / S273

页数：1

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