共 50 条
- [23] Treating adults with spinal muscular atrophy with nusinersen JOURNAL OF NEUROLOGY NEUROSURGERY AND PSYCHIATRY, 2020, 91 (11): : 1139 - 1139
- [27] Market access of Spinraza (Nusinersen) for spinal muscular atrophy: intellectual property rights, pricing, value and coverage considerations Gene Therapy, 2017, 24 : 539 - 541
- [28] New results for risdiplam in spinal muscular atrophy LANCET NEUROLOGY, 2022, 21 (12): : 1065 - 1066