Nusinersen Efficacy in Adults with Spinal Muscular Atrophy

被引:0
|
作者
Day, John [1 ]
Wolford, Connie
MacPherson, Chelsea [2 ]
Martens, William
McDermott, Michael [4 ]
Darras, Basil [5 ]
De Vivo, Darryl [6 ]
Cunningham, Zarazuela [7 ]
Finkel, Richard [8 ]
Zeineh, Michael [3 ]
Sampson, Jacinda
Hagerman, Katharine
Duong, Tina
机构
[1] Stanford Univ, Sch Med, Neurol & Pediat, Palo Alto, CA 94304 USA
[2] Rehabil Serv, Palo Alto, CA USA
[3] Stanford Univ, Radiol, Stanford, CA 94305 USA
[4] Univ Rochester, Neurol & Biostat, Rochester, NY USA
[5] Harvard Med Sch, ChildrenS Hosp Boston, Boston, MA 02115 USA
[6] Columbia Univ, Neurol & Pediat, New York, CA USA
[7] Childrens Hosp Philadelphia, Human Genet Div, Philadelphia, PA 19104 USA
[8] Nemours Hosp, Neurol, Orlando, FL USA
关键词
D O I
暂无
中图分类号
R74 [神经病学与精神病学];
学科分类号
摘要
S58.007
引用
收藏
页数:3
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