Micro-dystrophin Genes Bring Hope of an Effective Therapy for Duchenne Muscular Dystrophy

被引：16
|
作者：
Davies, Kay E. [1 ]
Guiraud, Simon [1 ]
机构：
[1] Univ Oxford, Dept Physiol Anat & Genet, MDUK Oxford Neuromuscular Ctr, Oxford OX1 3PT, England
来源：
MOLECULAR THERAPY | 2019年 / 27卷 / 03期
基金：
英国医学研究理事会;
关键词：
EXPRESSION; MODEL;
D O I：
10.1016/j.ymthe.2019.01.019
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：486 / 488
页数：3
相关论文
共 50 条
  • [41] Dystrophin analysis in carriers of Duchenne and Becker muscular dystrophy
    Hoogerwaard, EM
    Ginjaar, IB
    Bakker, E
    de Visser, M
    NEUROLOGY, 2005, 65 (12) : 1984 - 1986
  • [42] DYSTROPHIN AND THE INTEGRITY OF THE SARCOLEMMA IN DUCHENNE MUSCULAR-DYSTROPHY
    DUNCAN, CJ
    EXPERIENTIA, 1989, 45 (02): : 175 - 177
  • [43] Therapeutic restoration of dystrophin expression in Duchenne muscular dystrophy
    Wells, Dominic J.
    JOURNAL OF MUSCLE RESEARCH AND CELL MOTILITY, 2006, 27 (5-7) : 387 - 398
  • [44] Therapeutic Strategies for Dystrophin Replacement in Duchenne Muscular Dystrophy
    Happi Mbakam, Cedric
    Lamothe, Gabriel
    Tremblay, Jacques P.
    FRONTIERS IN MEDICINE, 2022, 9
  • [45] CHARACTERIZATION OF DYSTROPHIN IN CARRIERS OF DUCHENNE MUSCULAR-DYSTROPHY
    CLERK, A
    RODILLO, E
    HECKMATT, JZ
    DUBOWITZ, V
    STRONG, PN
    SEWRY, CA
    JOURNAL OF THE NEUROLOGICAL SCIENCES, 1991, 102 (02) : 197 - 205
  • [46] Cognition Associated with Dystrophin Deletion in Duchenne Muscular Dystrophy
    Cho, Soo Kyoung
    Moon, Jae Ho
    Lee, Sang Chul
    Yoo, Tae Won
    Ha, Young Ran
    Park, Young Bum
    Choi, Won Ah
    ANNALS OF REHABILITATION MEDICINE-ARM, 2006, 30 (03): : 225 - 229
  • [47] Effective correction of the mdx dystrophin gene mutation in the mouse model of Duchenne muscular dystrophy
    Todaro, M
    Wong, SHA
    Kita, M
    Quigley, AF
    Lowes, KN
    Marotta, R
    Cook, MJ
    Kornberg, AJ
    Kapsa, RMI
    NEUROMUSCULAR DISORDERS, 2005, 15 (9-10) : 714 - 714
  • [48] Establishing effective correction of the dystrophin mutation in the mdx mouse model of Duchenne muscular dystrophy
    Todaro, M
    Kita, M
    Quigley, A
    Lowes, K
    Marotta, R
    Cook, M
    Kornberg, AJ
    Kapsa, R
    JOURNAL OF GENE MEDICINE, 2005, 7 (08): : 1139 - 1139
  • [49] Are corticosteroids effective in Duchenne muscular dystrophy?
    Shah, Dheeraj
    INDIAN PEDIATRICS, 2008, 45 (05) : 401 - 402
  • [50] Dystrophin Gene Replacement and Gene Repair Therapy for Duchenne Muscular Dystrophy in 2016: An Interview
    Duan, Dongsheng
    HUMAN GENE THERAPY CLINICAL DEVELOPMENT, 2016, 27 (01) : 9 - 18
12345