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- [11] AAV Micro-Dystrophin Therapy Ameliorates Muscular Dystrophy in Young Adult Duchenne Muscular Dystrophy Dogs for Up to Thirty Months Following InjectionMOLECULAR THERAPY, 2018, 26 (05) : 5 - 5Hakim, Chady论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, NCATS, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAKodippili, Kasun论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAJenkins, Gregory论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAYang, Hsiao论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAPan, Xiufang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USALessa, Thais论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USA论文数: 引用数: h-index:机构:Emter, Craig论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAYue, Yongping论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAZhang, Keqing论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USADuan, Sean论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USAYao, Gang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USASchneider, Joel论文数: 0 引用数: 0 h-index: 0机构: Solid Biosci, Cambridge, MA USA Univ Missouri, NCATS, Columbia, MO USAYang, Nora论文数: 0 引用数: 0 h-index: 0机构: NCATS, Bethesda, MD USA Univ Missouri, NCATS, Columbia, MO USA论文数: 引用数: h-index:机构:Duan, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Columbia, MO USA Univ Missouri, NCATS, Columbia, MO USA
- [12] Single Systemic AAV Micro-Dystrophin Therapy Ameliorates Muscular Dystrophy in Young Adult Duchenne Muscular Dystrophy Dogs for Up to Two YearsMOLECULAR THERAPY, 2017, 25 (05) : 192 - 193Hakim, Chady H.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Natl Ctr Adv Translat Sci, Rockville, MD USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAKodippili, Kasun论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAJenkins, Gregory论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAYang, Hsiao T.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAPan, Xiufang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USALessa, Thais B.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USALeach, Stacey B.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Vet Med & Surg, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAEmter, Craig论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAYue, Yongping论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAZhang, Keqing论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USADuan, Sean论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAYao, Gang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Bioengn, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USASchneider, Joel S.论文数: 0 引用数: 0 h-index: 0机构: Solid GT, Cambridge, MA USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAYang, Nora N.论文数: 0 引用数: 0 h-index: 0机构: Natl Ctr Adv Translat Sci, Rockville, MD USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAChamberlain, Jeffrey S.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Neurol, Seattle, WA 98195 USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USADuan, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Dept Bioengn, Columbia, MO USA Univ Missouri, Dept Neurol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA
- [13] Micro-dystrophin gene therapy demonstrates long-term cardiac efficacy in a severe Duchenne muscular dystrophy modelMOLECULAR THERAPY-METHODS & CLINICAL DEVELOPMENT, 2023, 28 : 344 - 354Piepho, Arden B.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USALowe, Jeovanna论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USACumby, Laurel R.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USADorn, Lisa E.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USALake, Dana M.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USARastogi, Neha论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USAGertzen, Megan D.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USASturgill, Sarah L.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USAOdom, Guy L.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Neurol, Seattle, WA 98109 USA Univ Washington, Sen Paul D Wellstone Muscular Dystrophy Specialize, Seattle, WA 98109 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USAZiolo, Mark T.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USAAccornero, Federica论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USAChamberlain, Jeffrey S.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Dept Neurol, Seattle, WA 98109 USA Univ Washington, Sen Paul D Wellstone Muscular Dystrophy Specialize, Seattle, WA 98109 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USARafael-Fortney, Jill A.论文数: 0 引用数: 0 h-index: 0机构: Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Davis Heart & Lung Res Inst, Columbus, OH 43210 USA Ohio State Univ, Coll Med, Dept Physiol & Cell Biol, Columbus, OH 43210 USA
- [14] A Simplified Immune Suppression Scheme Leads to Persistent Micro-dystrophin Expression in Duchenne Muscular Dystrophy DogsHUMAN GENE THERAPY, 2012, 23 (02) : 202 - 209Shin, Jin-Hong论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USAYue, Yongping论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USASrivastava, Arun论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Dept Pediat, Gainesville, FL 32611 USA Univ Florida, Dept Mol Genet & Microbiol, Gainesville, FL 32611 USA Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USA论文数: 引用数: h-index:机构:Lai, Yi论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USADuan, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USA Univ Missouri, Dept Mol Microbiol & Immunol, Sch Med, MSB, Columbia, MO 65212 USA
- [15] Lifelong Outcomes of Systemic Adeno-Associated Virus Micro-Dystrophin Gene Therapy in a Murine Duchenne Muscular Dystrophy ModelHUMAN GENE THERAPY, 2023, 34 (9-10) : 449 - 458Wasala, Nalinda B.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAYue, Yongping论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USAHu, Bryan论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA论文数: 引用数: h-index:机构:Yao, Gang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Coll Engn, Dept Chem & Biomed Engn, Columbia, MO USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USADuan, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA Univ Missouri, Sch Med, Dept Neurol, Columbia, MO USA Univ Missouri, Coll Engn, Dept Chem & Biomed Engn, Columbia, MO USA Univ Missouri, Coll Vet Med, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, One Hosp Dr, Columbia, MO 65212 USA Univ Missouri, Dept Mol Microbiol & Immunol, Columbia, MO USA
- [16] Lentiviral Micro-dystrophin Gene Treatment into Late-stage mdx Mice for Duchenne Muscular Dystrophy DiseaseCURRENT GENE THERAPY, 2023, 23 (04) : 304 - 315Eren, Selen Abanuz论文数: 0 引用数: 0 h-index: 0机构: Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, Turkiye Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Kayisdagi St 32, TR-34755 Atasehir, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeTastan, Cihan论文数: 0 引用数: 0 h-index: 0机构: Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Uskudar Univ, Mol Biol & Genet Dept, Istanbul, Turkiye Uskudar Univ, Transgen Cell Technol & Epigenet Applicat & Res C, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeKaradeniz, Kevser Buse论文数: 0 引用数: 0 h-index: 0机构: Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeTuran, Raife Dilek论文数: 0 引用数: 0 h-index: 0机构: Yeditepe Univ, Dept Genet & Bioengn, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeCakirsoy, Didem论文数: 0 引用数: 0 h-index: 0机构: Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeKancagi, Derya Dilek论文数: 0 引用数: 0 h-index: 0机构: Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeYilmaz, Sevdican Ustun论文数: 0 引用数: 0 h-index: 0机构: Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Med Biotechnol Dept, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeOztatlici, Mustafa论文数: 0 引用数: 0 h-index: 0机构: Gaziantep Islam Sci & Technol Univ, Fac Med, Dept Histol & Embryol, Gaziantep, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeOztatlici, Hulya论文数: 0 引用数: 0 h-index: 0机构: Gaziantep Univ, Fac Med, Dept Histol & Embryol, Gaziantep, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeOzer, Samed论文数: 0 引用数: 0 h-index: 0机构: Acibadem Mehmet Ali Aydinlar Univ, Anim Applicat & Res Ctr, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeTumentemur, Gamze论文数: 0 引用数: 0 h-index: 0机构: Acibadem Mehmet Ali Aydinlar Univ, Vocat Sch Hlth Serv, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeBaykal, Ahmet Tarik论文数: 0 引用数: 0 h-index: 0机构: Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, TurkiyeOvali, Ercument论文数: 0 引用数: 0 h-index: 0机构: Acibadem Labcell Cellular Therapy Lab, Istanbul, Turkiye Acibadem Mehmet Ali Aydinlar Univ, Inst Hlth Sci, Dept Biochem & Mol Biol, Istanbul, Turkiye
- [17] What is the level of dystrophin expression required for effective therapy of Duchenne muscular dystrophy?JOURNAL OF MUSCLE RESEARCH AND CELL MOTILITY, 2019, 40 (02) : 141 - 150Wells, Dominic J.论文数: 0 引用数: 0 h-index: 0机构: Royal Vet Coll, Dept Comparat Biomed Sci, Neuromuscular Dis Grp, Royal Coll St, London NW1 0TU, England Royal Vet Coll, Dept Comparat Biomed Sci, Neuromuscular Dis Grp, Royal Coll St, London NW1 0TU, England
- [18] What is the level of dystrophin expression required for effective therapy of Duchenne muscular dystrophy?Journal of Muscle Research and Cell Motility, 2019, 40 : 141 - 150Dominic J. Wells论文数: 0 引用数: 0 h-index: 0机构: Royal Veterinary College,Neuromuscular Diseases Group, Department of Comparative Biomedical Sciences
- [19] Micro-dystrophin gene delivery for Duchenne Muscular Dystrophy: a double-blind, randomized placebo-controlled trialEUROPEAN JOURNAL OF NEUROLOGY, 2021, 28 : 289 - 289Mendell, J.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USASheih, P.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USASahenk, Z.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USALehman, K.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USALowes, L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAMiller, N.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAIammarino, M.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAAlfano, L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat & Neurol, Columbus, OH 43210 USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAWoods, J.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USASkura, C.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAMao, H.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAStaudt, L.论文数: 0 引用数: 0 h-index: 0机构: Ronald Reagan UCLA Med Ctr, Los Angeles, CA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAPotter, R.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAGriffin, D.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USALewis, S.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAHu, L.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USAUpadhyay, S.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USASingh, T.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USARodino-Klapac, L.论文数: 0 引用数: 0 h-index: 0机构: Sarepta Therapeut Inc, Cambridge, MA USA Nationwide Childrens Hosp, Res Inst, Ctr Gene Therapy, Columbus, OH USA
- [20] Intravenous Delivery of a Novel Micro-Dystrophin Vector Prevented Muscle Deterioration in Young Adult Canine Duchenne Muscular Dystrophy DogsMOLECULAR THERAPY, 2016, 24 : S198 - S199Hakim, Chady论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAPan, Xiufang论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAKodippili, Kasun论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USABlessa, Thais论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAYang, Hsiao T.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Coll Vet Med, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAYao, Gary论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Dept Bioengn, Coll Engn, Columbia, MO USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USALeach, Stacey论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Coll Vet Med, Dept Vet Med & Surg, Columbia, MO 65211 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAEmter, Craig论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Coll Vet Med, Dept Biomed Sci, Columbia, MO USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAYue, Yongping论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAZhang, Keqing论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USADuan, Sean X.论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAWasala, Nalinda论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA论文数: 引用数: h-index:机构:Legg, Charles R.论文数: 0 引用数: 0 h-index: 0机构: Solid GT LLC, Cambridge, MA USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USASchneider, Joel S.论文数: 0 引用数: 0 h-index: 0机构: Solid GT LLC, Cambridge, MA USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USAChamberlain, Jeffrey S.论文数: 0 引用数: 0 h-index: 0机构: Univ Washington, Sch Med, Dept Neurol, Seattle, WA USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USADuan, Dongsheng论文数: 0 引用数: 0 h-index: 0机构: Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA Univ Missouri, Sch Med, Dept Mol Microbiol & Immunol, Columbia, MO 65212 USA