CHARACTERISATION OF ADENO-ASSOCIATED VIRUS VECTOR PERSISTENCE AFTER LONG-TERM FOLLOW UP IN THE HAEMOPHILIA A DOG MODEL

被引：0

作者：

Batty, P. ^{[1
]}

Fong, S. ^{[2
]}

Franco, M. ^{[3
]}

Gil-Farina, I. ^{[3
]}

Sihn, C. -R. ^{[2
]}

Mo, A. ^{[1
]}

Harpell, L. ^{[1
]}

Hough, C. ^{[1
]}

Hurlbut, D. ^{[1
]}

Pender, A. ^{[1
]}

Winterborn, A. ^{[4
]}

Schmidt, M. ^{[3
]}

Lillicrap, D. ^{[1
]}

机构：

[1] Queens Univ, Dept Pathol & Mol Med, Kingston, ON, Canada

[2] BioMarin Pharmaceut, Novato, CA USA

[3] GeneWerk GmbH, Heidelberg, Germany

[4] Queens Univ, Anim Care Serv, Kingston, ON, Canada

来源：

HAEMOPHILIA | 2021年 / 27卷

关键词：

D O I：

暂无

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

ABS021

引用

页码：29 / 29

页数：1

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