CHARACTERISATION OF ADENO-ASSOCIATED VIRUS VECTOR PERSISTENCE AFTER LONG-TERM FOLLOW UP IN THE HAEMOPHILIA A DOG MODEL

被引:0
|
作者
Batty, P. [1 ]
Fong, S. [2 ]
Franco, M. [3 ]
Gil-Farina, I. [3 ]
Sihn, C. -R. [2 ]
Mo, A. [1 ]
Harpell, L. [1 ]
Hough, C. [1 ]
Hurlbut, D. [1 ]
Pender, A. [1 ]
Winterborn, A. [4 ]
Schmidt, M. [3 ]
Lillicrap, D. [1 ]
机构
[1] Queens Univ, Dept Pathol & Mol Med, Kingston, ON, Canada
[2] BioMarin Pharmaceut, Novato, CA USA
[3] GeneWerk GmbH, Heidelberg, Germany
[4] Queens Univ, Anim Care Serv, Kingston, ON, Canada
关键词
D O I
暂无
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
ABS021
引用
收藏
页码:29 / 29
页数:1
相关论文
共 50 条
  • [1] In vivo model of adeno-associated virus vector persistence and rescue
    Afione, SA
    Conrad, CK
    Kearns, WG
    Chunduru, S
    Adams, R
    Reynolds, TC
    Guggino, WB
    Cutting, GR
    Carter, BJ
    Flotte, TR
    JOURNAL OF VIROLOGY, 1996, 70 (05) : 3235 - 3241
  • [2] Long-term gene transfer in porcine myocardium after coronary infusion of an adeno-associated virus vector
    Kaplitt, MG
    Xiao, X
    Samulski, RJ
    Li, J
    Ojamaa, K
    Klein, IL
    Makimura, H
    Kaplitt, MJ
    Strumpf, RK
    Diethrich, EB
    ANNALS OF THORACIC SURGERY, 1996, 62 (06): : 1669 - 1676
  • [4] S/MAR Element Facilitates Episomal Long-Term Persistence of Adeno-Associated Virus Vector Genomes in Proliferating Cells
    Hagedorn, Claudia
    Schnoedt-Fuchs, Maria
    Boehme, Philip
    Abdelrazik, Heba
    Lipps, Hans J.
    Buening, Hildegard
    HUMAN GENE THERAPY, 2017, 28 (12) : 1169 - 1179
  • [5] Long Term Follow-Up of Adeno-Associated Virus Vector-Mediated Factor IX Gene Transfer in Mice
    Li, Hojun
    Schlachterman, Alexander
    Hamilton, Shari R.
    Zhang, Jim
    Bussadori, Giulio
    Arruda, Valder R.
    High, Katherine A.
    MOLECULAR THERAPY, 2009, 17 : S277 - S278
  • [6] Long-term functional adeno-associated virus-microdystrophin expression in the dystrophic CXMDj dog
    Koo, Taeyoung
    Okada, Takashi
    Athanasopoulos, Takis
    Foster, Helen
    Takeda, Shin'ichi
    Dickson, George
    JOURNAL OF GENE MEDICINE, 2011, 13 (09): : 497 - 506
  • [7] Long-term follow-up of liver-directed, adeno-associated, vector-mediated gene therapy in the canine model of hemophilia A
    Lillicrap, D.
    Harpell, L.
    Labelle, A.
    Webster, S.
    HAEMOPHILIA, 2012, 18 : 65 - 65
  • [8] Long-term follow-up of liver-directed, adeno-associated vector-mediated gene therapy in the canine model of hemophilia A
    Batty, P.
    Mo, A. M.
    Hurlbut, D.
    Ishida, J.
    Yates, B.
    Brown, C.
    Harpell, L.
    Hough, C.
    Pender, A.
    Rimmer, E. K.
    Infirri, S. Sardo
    Winterborn, A.
    Fong, S.
    Lillicrap, D.
    BLOOD, 2022, 140 (25) : 2672 - 2683
  • [9] Long-term persistence of gene expression from adeno-associated virus serotype 5 in the mouse airways
    S G Sumner-Jones
    L A Davies
    A Varathalingam
    D R Gill
    S C Hyde
    Gene Therapy, 2006, 13 : 1703 - 1713
  • [10] Long-term persistence of gene expression from adeno-associated virus serotype 5 in the mouse airways
    Sumner-Jones, S. G.
    Davies, L. A.
    Varathalingam, A.
    Gill, D. R.
    Hyde, S. C.
    GENE THERAPY, 2006, 13 (24) : 1703 - 1713