Neonatal gene therapy in a Mucopolysaccharidosis type I (MPSI) mouse model

被引：0

作者：

De Ponti, G. ^{[1
]}

Santi, L. ^{[1
]}

Dina, G. ^{[3
]}

Pievani, A. ^{[2
]}

Donsante, S. ^{[4
]}

Riminucci, M. ^{[4
]}

Corsi, A. ^{[4
]}

Sawamoto, K. ^{[5
]}

Passerini, L.

Annoni, A.

Gregori, S. ^{[1
]}

Biondi, A. ^{[6
]}

Quattrini, A. ^{[3
]}

Tomatsu, S. ^{[5
]}

Aiuti, A. ^{[1
,7
]}

Bernardo, M. E. ^{[1
,7
,8
]}

Serafini, M. ^{[2
]}

机构：

[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy

[2] Univ Milano Bicocca, Dept Pediat, M Tettamanti Res Ctr, Milan, Italy

[3] Ist Sci San Raffaele, Expt Neuropathol Unit, INSPE, Milan, Italy

[4] Sapienza Univ, Dept Mol Med, Rome, Italy

[5] Alfred duPont Hosp Children, Dept Biomed Res, Alfred, NY USA

[6] Univ Milano Bicocca, Dept Pediat, Milan, Italy

[7] Ist Sci San Raffaele, Pediat Immunohematol, Milan, Italy

[8] Univ Vita Salute San Raffaele, Milan, Italy

来源：

HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P550

引用

页码：A171 / A172

页数：2

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