Adeno-associated virus vector-mediated gene therapy in a murine model of mucopolysaccharidosis type I

被引：0
|
作者：
Belur, Lalitha [1 ,2 ]
deMorest, Zachary [3 ]
Whitley, Chester B. [1 ,4 ]
Low, Walter C. [3 ]
McIvor, R. Scott [1 ,2 ]
机构：
[1] Univ Minnesota, Inst Human Genet, Gene Therapy Program, Minneapolis, MN 55455 USA
[2] Univ Minnesota, Dept Genet Cell Biol & Dev, Minneapolis, MN USA
[3] Univ Minnesota, Dept Neurosurg, Minneapolis, MN 55455 USA
[4] Univ Minnesota, Dept Pediat, Minneapolis, MN 55455 USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2007年 / 92卷 / 04期
关键词：
D O I：
10.1016/j.ymgme.2007.08.016
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
11
引用
收藏
页码：S13 / S14
页数：2
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