Neonatal gene therapy in a Mucopolysaccharidosis type I (MPSI) mouse model

被引：0
|
作者：
De Ponti, G. [1 ]
Santi, L. [1 ]
Dina, G. [3 ]
Pievani, A. [2 ]
Donsante, S. [4 ]
Riminucci, M. [4 ]
Corsi, A. [4 ]
Sawamoto, K. [5 ]
Passerini, L.
Annoni, A.
Gregori, S. [1 ]
Biondi, A. [6 ]
Quattrini, A. [3 ]
Tomatsu, S. [5 ]
Aiuti, A. [1 ,7 ]
Bernardo, M. E. [1 ,7 ,8 ]
Serafini, M. [2 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy HSR TIGET, Milan, Italy
[2] Univ Milano Bicocca, Dept Pediat, M Tettamanti Res Ctr, Milan, Italy
[3] Ist Sci San Raffaele, Expt Neuropathol Unit, INSPE, Milan, Italy
[4] Sapienza Univ, Dept Mol Med, Rome, Italy
[5] Alfred duPont Hosp Children, Dept Biomed Res, Alfred, NY USA
[6] Univ Milano Bicocca, Dept Pediat, Milan, Italy
[7] Ist Sci San Raffaele, Pediat Immunohematol, Milan, Italy
[8] Univ Vita Salute San Raffaele, Milan, Italy
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P550
引用
收藏
页码：A171 / A172
页数：2
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