Long-Term Effects of Hematopoietic Stem Cell Gene Therapy in the Murine Model of Wiskott-Aldrich Syndrome: Persistence of Functional Correction of T Cells and Lack of Malignant Transformation

被引：0

作者：

Marangoni, Francesco ^{[1
,2
]}

Dupre, Loic ^{[1
]}

Scaramuzza, Samantha ^{[1
]}

Panaroni, Cristina ^{[1
]}

Trifari, Sara ^{[1
]}

Hernandez, Raisa Jofra ^{[1
]}

Thrasher, Adrian J. ^{[3
]}

Galy, Anne ^{[4
]}

Aiuti, Alessandro ^{[1
]}

Naldini, Luigi ^{[1
,2
]}

Roncarolo, Maria Grazia ^{[1
,2
]}

机构：

[1] Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy

[2] Univ Vita Salute San Raffaele, San Raffaele Sci Inst, Milan, Italy

[3] Inst Child Hlth, Mol Immunol Unit, London, England

[4] CNRS, UMR 8115, Evry, France

来源：

MOLECULAR THERAPY | 2006年 / 13卷

关键词：

D O I：

10.1016/j.ymthe.2006.08.081

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

引用

页码：S27 / S28

页数：2

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