Long-Term Effects of Hematopoietic Stem Cell Gene Therapy in the Murine Model of Wiskott-Aldrich Syndrome: Persistence of Functional Correction of T Cells and Lack of Malignant Transformation

被引：0
|
作者：
Marangoni, Francesco [1 ,2 ]
Dupre, Loic [1 ]
Scaramuzza, Samantha [1 ]
Panaroni, Cristina [1 ]
Trifari, Sara [1 ]
Hernandez, Raisa Jofra [1 ]
Thrasher, Adrian J. [3 ]
Galy, Anne [4 ]
Aiuti, Alessandro [1 ]
Naldini, Luigi [1 ,2 ]
Roncarolo, Maria Grazia [1 ,2 ]
机构：
[1] Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy
[2] Univ Vita Salute San Raffaele, San Raffaele Sci Inst, Milan, Italy
[3] Inst Child Hlth, Mol Immunol Unit, London, England
[4] CNRS, UMR 8115, Evry, France
来源：
MOLECULAR THERAPY | 2006年 / 13卷
关键词：
D O I：
10.1016/j.ymthe.2006.08.081
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
65
引用
收藏
页码：S27 / S28
页数：2
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