AAV-Mediated Gene Therapy Corrects the Severe Phenotype of Acid Ceramidase Deficient Mice

被引：0
|
作者：
Denard, Jerome [1 ,2 ]
Marinello, Martina [1 ,2 ]
Latournerie, Virginie [1 ,2 ]
Bonnin, Delphine [1 ,2 ]
Derome, Marion [1 ,2 ]
Martin, Samia [1 ,2 ]
Medin, Jeffrey A. [3 ]
Bello, Ana Buj [1 ,2 ]
机构：
[1] GENETHON, Evry, France
[2] Univ Evry, Univ Paris Saclay, Integrare Res Unit UMR S951, INSERM, Evry, France
[3] Med Coll Wisconsin, Dept Pediat & Biochem, Milwaukee, WI USA
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1598
引用
收藏
页码：749 / 750
页数：2
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