Development of Strategy for Multi-Dose Gene Therapy in Murine Model of Glycogen Storage Disease Type Ia

被引:0
|
作者
Arends, Charles [1 ,2 ]
Ameen, Yasir [1 ]
Lee, Young Mok [1 ,2 ]
机构
[1] Univ Connecticut, Sch Med, Dept Pediat, Farmington, CT USA
[2] Univ Connecticut, Genet & Genome Sci, Hlth Ctr, Farmington, CT USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
1199
引用
收藏
页码:571 / 572
页数:2
相关论文
共 50 条
  • [31] Hepatocellular adenoma in type Ia glycogen storage disease
    Kudo, M
    JOURNAL OF GASTROENTEROLOGY, 2001, 36 (01) : 65 - 66
  • [32] Tubular glycogen nuclei in a patient with glycogen storage disease type Ia
    Liang, Dandan
    Liu, Jing
    Zuo, Ke
    Gao, Erzhi
    Liang, Shaoshan
    Xu, Feng
    Zeng, Caihong
    KIDNEY INTERNATIONAL, 2024, 106 (06) : 1188 - 1188
  • [33] Mutation analysis in glycogen storage disease type Ia
    Meaney, C
    Lee, P
    Cranston, T
    Genet, S
    JOURNAL OF MEDICAL GENETICS, 2000, 37 : S73 - S73
  • [34] Hepatic Adenomas in Type Ia Glycogen Storage Disease
    不详
    GASTROENTEROLOGY, 2008, 135 (06) : 1817 - 1818
  • [35] Frequent hypoglycemia in Glycogen Storage Disease Type Ia
    Jirajariyavej, Teeranun
    Jain, Akshay Bhanwarlal
    Gianoukakis, Andrew George
    ENDOCRINE REVIEWS, 2014, 35 (03)
  • [36] Effects of DTX401 gene therapy administration on endocrine dysregulation in glycogen storage disease type Ia
    Derks, Terry G. J.
    Rodriguez-Buritica, David F.
    Riba-Wolman, Rebecca
    Rossi, Alessandro
    Loechner, Karen
    Mitragotri, Deepali
    Grimm, Andrew
    MOLECULAR GENETICS AND METABOLISM, 2024, 141 (04)
  • [37] Correction of glycogen storage disease type 1a in a mouse model by gene therapy
    Zingone, A
    Hiraiwa, H
    Pan, CJ
    Lin, BC
    Chen, HW
    Ward, JM
    Chou, JY
    JOURNAL OF BIOLOGICAL CHEMISTRY, 2000, 275 (02) : 828 - 832
  • [38] Systemic Correction of Murine Glycogen Storage Disease Type IV by an AAV-Mediated Gene Therapy
    Yi, Haiqing
    Zhang, Quan
    Brooks, Elizabeth D.
    Yang, Chunyu
    Thurberg, Beth L.
    Kishnani, Priya S.
    Sun, Baodong
    HUMAN GENE THERAPY, 2017, 28 (03) : 286 - 294
  • [39] Liver-Directed AAV Gene Transfer for Glycogen Storage Disease Type IA
    Jauze, Louisa
    Miliano, Alexane Cannella
    Silva, Marine
    Zitoun, Carine
    Mithieux, Gilles
    Ronzitti, Giuseppe
    Rajas, Fabienne
    MOLECULAR THERAPY, 2021, 29 (04) : 238 - 238
  • [40] REGRESSION OF HEPATIC ADENOMAS IN TYPE IA GLYCOGEN-STORAGE DISEASE WITH DIETARY THERAPY
    PARKER, P
    BURR, I
    SLONIM, A
    GHISHAN, FK
    GREENE, H
    GASTROENTEROLOGY, 1981, 81 (03) : 534 - 536