Effects of DTX401 gene therapy administration on endocrine dysregulation in glycogen storage disease type Ia

被引：0
|
作者：
Derks, Terry G. J. [1 ]
Rodriguez-Buritica, David F. [2 ]
Riba-Wolman, Rebecca [3 ]
Rossi, Alessandro [4 ]
Loechner, Karen [3 ]
Mitragotri, Deepali [5 ]
Grimm, Andrew [5 ]
机构：
[1] Univ Groningen, Univ Med Ctr Groningen, Beatrix Childrens Hosp, Sect Metab Dis, Groningen, Netherlands
[2] Univ Texas McGovern Med Sch, Houston, TX USA
[3] Univ Connecticut, Farmington, CT USA
[4] Univ Naples Federico II, Dept Translat Med, Naples, Italy
[5] Ultragenyx Pharmaceut Inc, Novato, CA USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2024年 / 141卷 / 04期
关键词：
D O I：
10.1016/j.ymgme.2024.108313
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
Poster # 1
引用
收藏
页数：1
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