Improvements in Health-Related Quality of Life after Exagamglogene Autotemcel in Patients with Severe Sickle Cell Disease

被引：2
|
作者：
Sharma, Akshay [1 ]
Frangoul, Haydar [2 ]
Mapara, Markus [3 ]
Imren, Suzan [4 ]
Li, Nanxin [4 ]
Liu, Tina [4 ]
Rubin, Jaime [4 ]
Shi, Daoyuan [4 ]
Hobbs, William [4 ]
Grupp, Stephan [5 ]
机构：
[1] St Jude Childrens Res Hosp, Memphis, TN USA
[2] TriStar Centennial, Sarah Cannon Res Inst, Childrens Hosp, Nashville, TN USA
[3] Columbia Univ, Div Hematol Oncol, Dept Med, New York, NY USA
[4] Vertex Pharmaceut, Boston, MA USA
[5] Childrens Hosp Philadelphia, Div Oncol, Philadelphia, PA USA
来源：
BLOOD | 2023年 / 142卷
关键词：
D O I：
10.1182/blood-2023-190203
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页数：3
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