Design and Objectives of the Acorn Study: A Non-Interventional Study Evaluating Long-term Safety in Achondroplasia Patients Treated with Vosoritide

被引：0
|
作者：
Pimenta, Jeanne M. [1 ]
Cohen, Shelda [1 ]
Mukherjee, Swati [1 ]
Fettes, Fiona [1 ]
Jayaram, Kala [2 ]
Lausch, Ekkehart [3 ]
机构：
[1] BioMarin UK Ltd, London, England
[2] BioMarin Pharmaceut Inc, Novato, CA USA
[3] Univ Freiburg, Sect Pediat Genet, Ctr Pediat, Freiburg, Germany
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2023年 / 96卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
T8
引用
收藏
页码：127 / 128
页数：2
相关论文
共 50 条
  • [21] Clinical characterization of long-term multiple sclerosis (COLuMbus) patients in Argentina: A cross-sectional non-interventional study
    Deri, Norma
    Barboza, Andres
    Vrech, Carlos
    Rey, Roberto
    Burgos, Marcos
    Fiol, Marcela
    CalvoVildoso, Cristian
    Patrucco, Liliana
    Jose, Gustavo
    Aliberti, Paula
    Chirico, Daniela
    Federico, Maria B.
    Seifer, Gustavo
    Piedrabuena, Raul
    MULTIPLE SCLEROSIS AND RELATED DISORDERS, 2024, 83
  • [22] X-Tab: Non-interventional long-term study of omalizumab therapy in severe allergic asthmatic patients in Germany
    Schreiber, J.
    Mailaender, C.
    ALLERGY, 2018, 73 : 203 - 204
  • [23] Design of a non-interventional post-marketing study to assess the long-term safety and effectiveness of ocrelizumab in German real world multiple sclerosis cohorts - the CONFIDENCE study protocol
    Dirks, Petra
    Zingler, Vera
    Leemhuis, Jost
    Berthold, Heike
    Hieke-Schulz, Stefanie
    Wormser, David
    Ziemssen, Tjalf
    BMC NEUROLOGY, 2020, 20 (01)
  • [24] Design of a non-interventional post-marketing study to assess the long-term safety and effectiveness of ocrelizumab in German real world multiple sclerosis cohorts – the CONFIDENCE study protocol
    Petra Dirks
    Vera Zingler
    Jost Leemhuis
    Heike Berthold
    Stefanie Hieke-Schulz
    David Wormser
    Tjalf Ziemssen
    BMC Neurology, 20
  • [25] Impact of Age and Type of Underlying Disease on Long-Term Safety and Efficacy in Patients with Transfusional Hemosiderosis Treated with Deferasirox: Results from a 3-Year Non-Interventional Study (SENTINEL)
    Elalfy, Mohsen
    Inusa, Baba
    Beneitez, David
    Xicoy, Blanca
    Nieto, Maria Soledad Duran
    Bruederle, Andreas
    Azmon, Amin
    El-Beshlawy, Amal
    BLOOD, 2016, 128 (22)
  • [26] QUALITY: A NON-INTERVENTIONAL STUDY EVALUATING QUALITY OF LIFE IN SCHIZOPHRENIC PATIENTS TREATED WITH ATYPICAL ANTIPSYCHOTICS IN THE AMBULATORY SETTING
    Peuskens, J.
    Fontaine, E.
    Vanlerberghe, T.
    EUROPEAN PSYCHIATRY, 2011, 26
  • [27] Alemtuzumab post authorization safety study (PASS) study design: Evaluating the long-term safety profile of alemtuzumab in patients with RRMS
    Montalban, X.
    Rodriguez-Antiguedad, A.
    Forner, M.
    Colilla, S.
    Margolin, D. H.
    EUROPEAN JOURNAL OF NEUROLOGY, 2017, 24 : 320 - 320
  • [28] Study design of PANGAEA 2.0, a non-interventional study on RRMS patients to be switched to fingolimod
    Tjalf Ziemssen
    Raimar Kern
    Christian Cornelissen
    BMC Neurology, 16
  • [29] Retrospective, Non-interventional, Multi-centre Study Evaluating Safety of Fingolimod in Patients with Multiple Sclerosis in Taiwan
    Yang, C. C.
    Ro, L. S.
    Tsai, N. W.
    Lin, C. C.
    Huang, W. N.
    Tsai, C. P.
    Lin, T. S.
    Su, J. J.
    Huang, C. C.
    MULTIPLE SCLEROSIS JOURNAL, 2019, 25 (03) : 459 - 459
  • [30] Study design of PANGAEA 2.0, a non-interventional study on RRMS patients to be switched to fingolimod
    Ziemssen, Tjalf
    Kern, Raimar
    Cornelissen, Christian
    BMC NEUROLOGY, 2016, 16
12345