Design and Objectives of the Acorn Study: A Non-Interventional Study Evaluating Long-term Safety in Achondroplasia Patients Treated with Vosoritide

被引：0
|
作者：
Pimenta, Jeanne M. [1 ]
Cohen, Shelda [1 ]
Mukherjee, Swati [1 ]
Fettes, Fiona [1 ]
Jayaram, Kala [2 ]
Lausch, Ekkehart [3 ]
机构：
[1] BioMarin UK Ltd, London, England
[2] BioMarin Pharmaceut Inc, Novato, CA USA
[3] Univ Freiburg, Sect Pediat Genet, Ctr Pediat, Freiburg, Germany
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2023年 / 96卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
T8
引用
收藏
页码：127 / 128
页数：2
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