Design and Objectives of the Acorn Study: A Non-Interventional Study Evaluating Long-term Safety in Achondroplasia Patients Treated with Vosoritide

被引：0
|
作者：
Pimenta, Jeanne M. [1 ]
Cohen, Shelda [1 ]
Mukherjee, Swati [1 ]
Fettes, Fiona [1 ]
Jayaram, Kala [2 ]
Lausch, Ekkehart [3 ]
机构：
[1] BioMarin UK Ltd, London, England
[2] BioMarin Pharmaceut Inc, Novato, CA USA
[3] Univ Freiburg, Sect Pediat Genet, Ctr Pediat, Freiburg, Germany
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2023年 / 96卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
T8
引用
收藏
页码：127 / 128
页数：2
相关论文
共 50 条
  • [1] ICHIBAN, a non-interventional study evaluating tocilizumab long-term effectiveness and safety in patients with active rheumatoid arthritis
    Specker, C.
    Alberding, A.
    Aringer, M.
    Burmester, G-R
    Flacke, J-P
    Hofmann, M. W.
    Kaestner, P.
    Kellner, H.
    Moosig, F.
    Sieburg, M.
    Tony, H-P
    Fliedner, G.
    CLINICAL AND EXPERIMENTAL RHEUMATOLOGY, 2021, 39 (02) : 319 - 328
  • [2] NON-INTERVENTIONAL POST-MARKETING SAFETY STUDY ON THE LONG-TERM SAFETY OF HYQVIA (GLOBAL)
    Fielhauer, Katharina
    Nagy, Andras
    Rabbat, Christopher
    McCoy, Barbara
    Leibl, Heinz
    Yel, Leman
    JOURNAL OF CLINICAL IMMUNOLOGY, 2016, 36 (03) : 268 - 268
  • [3] Assessment of Immunoglobulins in a Long-Term Non-Interventional Study (SIGNS Study). Rationale, Design, and Methods
    Kirch, Wilhelm
    Gold, Ralf
    Hensel, Manfred
    Fasshauer, Maria
    Pittrow, David
    Huscher, Doerte
    Reiser, Marcel
    Stangel, Martin
    Baumann, Ulrich
    Borte, Michael
    MEDIZINISCHE KLINIK, 2010, 105 (09) : 647 - 651
  • [4] Evaluation of Long-Term Safety of Latanoprost in Pediatric Populations: Design and Rationale of an Ongoing Non-Interventional Cohort Study
    Xu, Wanning
    Huang, Kui
    Sultan, Marla
    Zhang, Min
    PHARMACOEPIDEMIOLOGY AND DRUG SAFETY, 2013, 22 : 349 - 349
  • [5] Non-Interventional Post-Authorization Safety Study (PASS) on the Long-Term Safety of HYQVIA® (IGHY)
    Fielhauer, K.
    Nikolov, N.
    Hermann, C.
    Nagy, A.
    Schiff, R. I.
    JOURNAL OF CLINICAL IMMUNOLOGY, 2014, 34 : S294 - S294
  • [6] Study design of a non-interventional registry study to establish long-term safety and pharmaco-economic data on fingolimod (Gilenya®) in multiple sclerosis patients (PANGAEA)
    van Lokven, T.
    Kempcke, R.
    Ziemssen, T.
    Meergans, M.
    MULTIPLE SCLEROSIS JOURNAL, 2011, 17 : S213 - S214
  • [7] QUALITY: a non-interventional study evaluating QOL in schizophrenic patients treated with atypical antipsychotics
    Peuskens, J.
    Taeter, C.
    Duquenne, V.
    EUROPEAN NEUROPSYCHOPHARMACOLOGY, 2010, 20 : S478 - S478
  • [8] Real-world non-interventional long-term post-authorisation safety study of ruxolitinib in myelofibrosis
    Barraco, Fiorenza
    Grei, Richard
    Herbrecht, Raoul
    Schmidt, Burkhard
    Reiter, Andreas
    Willenbacher, Wolfgang
    Raymakers, Reinier
    Liersch, Rudiger
    Wroclawska, Monika
    Pack, Robert
    Burock, Karin
    Karumanchi, Divyadeep
    Gisslinger, Heinz
    BRITISH JOURNAL OF HAEMATOLOGY, 2020, 191 (05) : 764 - 774
  • [9] Long-Term Treatment of chronic schizophrenic Patients with Flupentixol decanoate Results of a prospective non-interventional Study
    Laux, Gerd
    Steinmann, Carsten
    Glaser, Thomas
    PSYCHOPHARMAKOTHERAPIE, 2010, 17 (06): : 274 - +
  • [10] The PANGAEA study design - a prospective, multicenter, non-interventional, long-term study on fingolimod for the treatment of multiple sclerosis in daily practice
    Ziemssen, Tjalf
    Kern, Raimar
    Cornelissen, Christian
    BMC NEUROLOGY, 2015, 15
12345