Muopolysaccharidosis Type I Skeletal Alterations and Cross Correction in an Ex Vivo Gene Therapy Approach

被引：0
|
作者：
Santi, Ludovica [1 ]
Crippa, Stefania [1 ]
Capo, Valentina [1 ]
Penna, Sara [1 ]
De Ponti, Giada [1 ]
Alberti, Gaia [1 ]
Berti, Margherita [1 ]
Basini, Tommaso [1 ]
Consiglieri, Giulia [2 ]
Tucci, Francesca [2 ]
Riminucci, Mara [3 ]
Corsi, Alessandro [3 ]
Barbero, Andrea [4 ]
Lopa, Silvia [5 ]
Martin, Ivan [4 ]
Moretti, Matteo [5 ]
Gentner, Bernhard [1 ]
Aiuti, Alessandro [1 ]
Villa, Anna [1 ]
Bernardo, Maria Ester [1 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy SR TIGET, Milan, Italy
[2] Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy
[3] Sapienza Univ, Dept Mol Med, Rome, Italy
[4] Tissue Engn Dept Biomed, Basel, Switzerland
[5] Cell & Tissue Engn Lab, Milan, Italy
来源：
MOLECULAR THERAPY | 2023年 / 31卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
1514
引用
收藏
页码：712 / 713
页数：2
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