Skeletal Damage and Cross-correction after ex-vivo Gene Therapy in Mucopolysaccharidosis type I Hurler

被引：0
|
作者：
Santi, Ludovica [1 ]
Crippa, Stefania [1 ]
Capo, Valentina [1 ]
Penna, Sara [1 ]
Savoia, Evelyn [1 ]
De Ponti, Giada [1 ]
Alberti, Gaia [1 ]
Berti, Margherita [1 ]
Ceriotti, Selene [1 ]
Consiglieri, Giulia [2 ]
Tucci, Francesca [2 ]
Riminucci, Mara [3 ]
Corsi, Alessandro [3 ]
Barbero, Andrea [4 ]
Martin, Ivan [4 ]
Sanvito, Francesca [5 ]
Norata, Rossana [5 ]
Rocchi, Martina [5 ]
Bolamperti, Simona [6 ]
Villa, Isabella [6 ]
Aiuti, Alessandro [1 ]
Villa, Anna [1 ]
Bernardo, Maria Ester [1 ]
机构：
[1] San Raffaele Telethon Inst Gene Therapy, Milan, Italy
[2] IRCCS San Raffaele Sci Inst, Pediatr Immunohematol & Bone Marrow Transplantat, Milan, Italy
[3] Sapienza Univ, Dept Mol Med, Rome, Italy
[4] Univ Basel Hosp, Tissue Engn Dept Biomed, Basel, Switzerland
[5] IRCCS San Raffaele Sci Inst, GLP San Raffaele Telethon Inst Gene Therapy, Milan, Italy
[6] IRCCS San Raffaele Sci Inst, Osteoporosis & Bone & Mineral Metab Unit, Milan, Italy
来源：
JOURNAL OF BONE AND MINERAL RESEARCH | 2024年 / 39卷
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
FRI-166
引用
收藏
页码：30 / 31
页数：2
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