Ex-vivo Autologous Haematopoietic Stem Cell Gene Therapy in Mucopolysaccharidosis Type IIIA

被引:0
|
作者
Kinsella, Jane [1 ]
Jones, Simon [2 ]
Church, Heather [3 ]
Jones, Ceri [3 ]
Ellison, Stuart [4 ]
Booth, Claire [5 ]
Buckland, Karen [5 ]
Rico, Diego Leon [5 ]
Bigger, Brian [4 ]
Thrasher, Adrian J. [5 ]
Wynn, Robert [1 ]
机构
[1] MFT, Royal Manchester Childrens Hosp, Manchester, Lancs, England
[2] MFT, Manchester Ctr Genom Med, Manchester, Lancs, England
[3] MFT, Manchester Ctr Genom Med, Manchester, Lancs, England
[4] Univ Manchester, Manchester, Lancs, England
[5] UCL, Great Ormond St Inst Child Hlth, London, England
关键词
D O I
暂无
中图分类号
Q6 [生物物理学];
学科分类号
071011 ;
摘要
P185
引用
收藏
页码:320 / 320
页数:1
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