共 50 条
- [1] Case report of the first patient treated with ex-vivo autologous haematopoietic stem cell gene therapy transplant in mucopolysaccharidosis type IIIAMOLECULAR GENETICS AND METABOLISM, 2020, 129 (02) : S90 - S90Kinsella, Jane Louise论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandChurch, Heather论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandOgden, Wendy论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandJones, Ceri论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandRivat, Christine论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandThrasher, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandSnell, Katie论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandLeon-Rico, Diego论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandVaz, Fred论文数: 0 引用数: 0 h-index: 0机构: Amsterdam Med Ctr, Amsterdam, Netherlands Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandWijburg, Frits论文数: 0 引用数: 0 h-index: 0机构: Amsterdam Med Ctr, Amsterdam, Netherlands Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandJones, Simon论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBigger, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandWynn, Robert论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, England
- [2] BIOCHEMICAL ENGRAFTMENT AND CLINICAL OUTCOMES OF EX-VIVO AUTOLOGOUS STEM CELL GENE THERAPY FOR MUCOPOLYSACCHARIDOSIS TYPE IIIABONE MARROW TRANSPLANTATION, 2023, 58 (SUPP1) : 62 - 63Guha, Anthea论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandWynn, Robert论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandBigger, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandKinsella, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, England Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, England论文数: 引用数: h-index:机构:Potter, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, England论文数: 引用数: h-index:机构:Thrasher, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandBooth, Kathryn论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandIzotova, Natalia论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandWeisberg, Daniel论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandChurch, Heather论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandTylee, Karen论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandBrammeier, Kathryn论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandJones, Simon论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandSadegholnejat, Atusa论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, EnglandJones, Ceri论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hopsital, Manchester, Lancs, England Royal Manchester Childrens Hopsital, Manchester, Lancs, England
- [3] Biochemical Engraftment and Clinical Outcomes Following Ex-Vivo Autologous Stem Cell Gene Therapy for Mucopolysaccharidosis Type IIIABLOOD, 2022, 140 : 1897 - 1898Wynn, Robert F.论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandKinsella, Jane L.论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Paediat Bone Marrow Transplant, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandHolley, Rebecca J.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Stem Cell & Neuropathies, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandPotter, Jane论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, London, England Great Ormond St Hosp NHS Trust, London, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBooth, Claire论文数: 0 引用数: 0 h-index: 0机构: Inst Child Hlth, London, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Hosp, London, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandIzotova, Natalia论文数: 0 引用数: 0 h-index: 0机构: UCL Great Ormond St Inst Child Hlth, Mol & Cellular Immunol Unit, London, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandWeisberg, Daniel论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandChurch, Heather J.论文数: 0 引用数: 0 h-index: 0机构: Manchester Fdn Trust, Willink Biochem Genet Unit, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandTylee, Karen L.论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Willink Biochem Genet Unit, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBrammeier, Kathryn L.论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Willink Biochem Genet Unit, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Transplantat Lab, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Transplantat Lab, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandSadegholnejat, Atusa论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Transplantat Lab, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandJones, Simon A.论文数: 0 引用数: 0 h-index: 0机构: Manchester NHS Fdn Trust, Willink Biochem Genet Unit, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandEllison, Stuart论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Stem Cell & Neurotherapies Lab, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, EnglandBigger, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Stem Cell & Neurotherapies, Manchester, Lancs, England Manchester Univ NHS Fdn Trust, Royal Manchester Childrens Hosp, Manchester, Lancs, England
- [4] Clinical outcomes and sustained biochemical engraftment following ex-vivo autologous stem cell gene therapy for mucopolysaccharidosis type IIIAMOLECULAR GENETICS AND METABOLISM, 2024, 141 (02)Jones, Simon论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, England St Marys Hosp, Manchester, EnglandKinsella, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, England St Marys Hosp, Manchester, EnglandHolley, Rebecca J.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, England St Marys Hosp, Manchester, England论文数: 引用数: h-index:机构:Booth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England St Marys Hosp, Manchester, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England St Marys Hosp, Manchester, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester, England St Marys Hosp, Manchester, England论文数: 引用数: h-index:机构:Church, Heather J.论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester, England St Marys Hosp, Manchester, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester, England St Marys Hosp, Manchester, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester, England St Marys Hosp, Manchester, England论文数: 引用数: h-index:机构:Searle, Rachel论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, England St Marys Hosp, Manchester, EnglandEllison, Stuart M.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, England St Marys Hosp, Manchester, EnglandWynn, Robert论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester, England St Marys Hosp, Manchester, EnglandBigger, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, England St Marys Hosp, Manchester, England
- [5] Sustained biochemical engraftment and early clinical outcomes following ex-vivo autologous stem cell gene therapy for mucopolysaccharidosis type IIIAMOLECULAR GENETICS AND METABOLISM, 2023, 138 (02) : 68 - 69Jones, Simon论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandKinsella, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, England论文数: 引用数: h-index:机构:Potter, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandBooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Paediat Neuropsychol, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandChurch, Heather J.论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, St Marys Hosp, Willink Biochem Genet Unit, Manchester Ctr Genom Med, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandBrammeier, Kathryn L.论文数: 0 引用数: 0 h-index: 0机构: Manchester Univ NHS Fdn Trust, Manchester Ctr Genom Med, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandEllison, Stuart M.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Stemcell & Neurotherapies Grp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandBigger, Brian论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandWynn, Robert论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, England
- [6] Ex-Vivo Autologous Stem Cell Gene Therapy Clinical Trial for Mucopolysaccharidosis Type IIIA: Trial in Progress-NCT04201405BLOOD, 2020, 136Kinsella, Jane L.论文数: 0 引用数: 0 h-index: 0Wynn, Robert F.论文数: 0 引用数: 0 h-index: 0Bigger, Brian论文数: 0 引用数: 0 h-index: 0Thrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0Booth, Claire论文数: 0 引用数: 0 h-index: 0Buckland, Karen论文数: 0 引用数: 0 h-index: 0Izotova, Natalia论文数: 0 引用数: 0 h-index: 0Rust, Stewart论文数: 0 引用数: 0 h-index: 0Weisberg, Daniel论文数: 0 引用数: 0 h-index: 0Church, Heather J.论文数: 0 引用数: 0 h-index: 0Brammeier, Kathryn L.论文数: 0 引用数: 0 h-index: 0Tylee, Karen L.论文数: 0 引用数: 0 h-index: 0Jones, Ceri论文数: 0 引用数: 0 h-index: 0Lee, Helena论文数: 0 引用数: 0 h-index: 0Ford, Laura论文数: 0 引用数: 0 h-index: 0Sadegholnejat, Atusa论文数: 0 引用数: 0 h-index: 0Ellison, Stuart论文数: 0 引用数: 0 h-index: 0Jones, Simon A.论文数: 0 引用数: 0 h-index: 0
- [7] Ex-vivo autologous stem cell gene therapy clinical trial for mucopolysaccharidosis type IIIA: Update on phase I/II clinical trialMOLECULAR GENETICS AND METABOLISM, 2021, 132 (02) : S56 - S57Kinsella, Jane Louise论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandJones, Simon论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandThrasher, Adrian J.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Mol & Cellular Immunol, London, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandBooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Mol & Cellular Immunol, London, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandBuckland, Karen F.论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Mol & Cellular Immunol, London, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandIzotova, Natalia论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, Mol & Cellular Immunol, London, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Paediat Neuropsychol, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandWeisberg, Daniel论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Paediat Neuropsychol, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandChurch, Heather J.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandTylee, Karen L.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandBrammeier, Kathryn L.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandJones, Ceri论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester Ctr Genom Med, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Transplantat Lab, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Transplantat Lab, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandSadegholnejat, Atusa论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Transplantat Lab, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England论文数: 引用数: h-index:机构:Bigger, Brian W.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, EnglandWynn, Robert F.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England Royal Manchester Childrens Hosp, Bone Marrow Transplantat Unit, Manchester, Lancs, England
- [8] Clinical Trial Update: Ex-vivo autologous haematopoietic stem cell gene therapy in MPSIIIAHUMAN GENE THERAPY, 2021, 32 (19-20) : A139 - A140Jones, S. A.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandKinsella, J. L.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandPotter, J.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandThrasher, A. J.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Inst Child Hlth, London, England Univ Manchester, Manchester, Lancs, EnglandBooth, C.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Inst Child Hlth, London, England Univ Manchester, Manchester, Lancs, EnglandBuckland, K. F.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Inst Child Hlth, London, England Univ Manchester, Manchester, Lancs, EnglandIzotova, N.论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Inst Child Hlth, London, England Univ Manchester, Manchester, Lancs, EnglandRust, S.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandWeisberg, D.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandChurch, H. J.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandTylee, K. L.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandBrammeier, K. L.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandJones, C.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandLee, H.论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandFord, L.论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandSadegholnejat, A.论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandHolley, R. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England论文数: 引用数: h-index:机构:Bigger, B. W.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandWynn, R. F.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England
- [9] Clinical trial update: Ex-vivo autologous hematopoietic stem cell gene therapy in MPS IIIAMOLECULAR GENETICS AND METABOLISM, 2022, 135 (02) : S63 - S64Jones, Simon A.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandKinsella, Jane L.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandPotter, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandThrasher, Adrian论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandBooth, Claire论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandBuckland, Karen论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandIzotova, Natalia论文数: 0 引用数: 0 h-index: 0机构: UCL, Great Ormond St Inst Child Hlth, London, England St Marys Hosp, Manchester, Lancs, EnglandRust, Stewart论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandWeisberg, Daniel论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandChurch, Heather论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandTylee, Karen论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandLee, Helena论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandFord, Laura论文数: 0 引用数: 0 h-index: 0机构: Manchester Royal Infirm, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandHolley, Rebecca J.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, England论文数: 引用数: h-index:机构:Bigger, Brian W.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, EnglandWynn, Robert F.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester, Lancs, England St Marys Hosp, Manchester, Lancs, England
- [10] Lentiviral vector enhanced haematopoietic stem cell gene therapy for mucopolysaccharidosis type IIIABONE MARROW TRANSPLANTATION, 2011, 46 : S316 - S316论文数: 引用数: h-index:机构:Wilkinson, F.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandLangford-Smith, K. J.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandSergijenko, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandBennett, W.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, EnglandHowe, S.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Univ Manchester, Manchester, Lancs, EnglandThrasher, A.论文数: 0 引用数: 0 h-index: 0机构: UCL, London, England Univ Manchester, Manchester, Lancs, EnglandJones, S.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester M13 0JH, Lancs, England Univ Manchester, Manchester, Lancs, EnglandWraith, J. E.论文数: 0 引用数: 0 h-index: 0机构: St Marys Hosp, Manchester M13 0JH, Lancs, England Univ Manchester, Manchester, Lancs, EnglandWynn, R.论文数: 0 引用数: 0 h-index: 0机构: Royal Manchester Childrens Hosp, Manchester M27 1HA, Lancs, England Univ Manchester, Manchester, Lancs, EnglandBigger, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Manchester, Manchester, Lancs, England Univ Manchester, Manchester, Lancs, England