Muopolysaccharidosis Type I Skeletal Alterations and Cross Correction in an Ex Vivo Gene Therapy Approach

被引：0

作者：

Santi, Ludovica ^{[1
]}

Crippa, Stefania ^{[1
]}

Capo, Valentina ^{[1
]}

Penna, Sara ^{[1
]}

De Ponti, Giada ^{[1
]}

Alberti, Gaia ^{[1
]}

Berti, Margherita ^{[1
]}

Basini, Tommaso ^{[1
]}

Consiglieri, Giulia ^{[2
]}

Tucci, Francesca ^{[2
]}

Riminucci, Mara ^{[3
]}

Corsi, Alessandro ^{[3
]}

Barbero, Andrea ^{[4
]}

Lopa, Silvia ^{[5
]}

Martin, Ivan ^{[4
]}

Moretti, Matteo ^{[5
]}

Gentner, Bernhard ^{[1
]}

Aiuti, Alessandro ^{[1
]}

Villa, Anna ^{[1
]}

Bernardo, Maria Ester ^{[1
]}

机构：

[1] San Raffaele Telethon Inst Gene Therapy SR TIGET, Milan, Italy

[2] Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy

[3] Sapienza Univ, Dept Mol Med, Rome, Italy

[4] Tissue Engn Dept Biomed, Basel, Switzerland

[5] Cell & Tissue Engn Lab, Milan, Italy

来源：

MOLECULAR THERAPY | 2023年 / 31卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

1514

引用

页码：712 / 713

页数：2

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