Engineering isogenic neuronal models of ATXN3 knockout in Machado-Joseph Disease patient cells by CRISPR/Cas9

被引：0
|
作者：
Fernandes, A. R. [1 ,2 ,3 ]
Adao, D. [1 ,3 ]
Lopes, S. M. [1 ,2 ,3 ]
Henriques, D. [1 ,2 ,3 ]
Pena, F. [1 ,2 ,3 ]
Dias, M. [1 ,3 ]
Santana, M. M. [1 ,2 ,3 ]
Perdigao, P. [1 ,2 ,3 ]
Almeida, L. P. [1 ,3 ,4 ]
机构：
[1] Univ Coimbra, Ctr Neurosci & Cell Biol, Coimbra, Portugal
[2] Univ Coimbra, Inst Interdisciplinary Res, Coimbra, Portugal
[3] Univ Coimbra, Ctr Innovat Biomed & Biotechnol, Coimbra, Portugal
[4] Univ Coimbra, Fac Pharm, Coimbra, Portugal
来源：
HUMAN GENE THERAPY | 2024年 / 35卷 / 3-4期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P297
引用
收藏
页码：A142 / A143
页数：2
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