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- [41] Gene therapy for Wnt signalling-related retinal detachment: Intravitreal injection of AAV.NDP is an effective treatment for vascular exudation in a mouse model of familial exudative vitreoretinopathy (FEVR)/ Coats diseaseINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2023, 64 (08)Wawrzynski, James论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England UCL, Inst Child Hlth, London, EnglandHenderson, Robert论文数: 0 引用数: 0 h-index: 0机构: Great Ormond St Hosp Children NHS Fdn Trust, London, England Moorfields Eye Hosp NHS Fdn Trust, London, England UCL, Inst Child Hlth, London, EnglandPauzuolyte, Valda论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England UCL, Inst Child Hlth, London, EnglandPatel, Aara论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England Great Ormond St Hosp Children NHS Fdn Trust, London, England UCL, Inst Child Hlth, London, EnglandCoombe-Tennant, Oliver论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England UCL, Inst Child Hlth, London, EnglandMoulding, Dale论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England UCL, Inst Child Hlth, London, EnglandSowden, Jane C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Inst Child Hlth, London, England UCL, Inst Child Hlth, London, England
- [42] Efficient Transduction of Tyrosine-to-Phenylalanine Mutated AAV2 Vectors Carrying Human ND4 Gene and Biodistribution Following Intravitreal Delivery in a Rodent Model - A Gene Therapy for Leber Hereditary Optic NeuropathyMOLECULAR THERAPY, 2012, 20 : S169 - S169Koilkonda, Rajeshwari D.论文数: 0 引用数: 0 h-index: 0机构: Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USA Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USAHauswirth, William W.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Gainesville, FL USA Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USAChiodo, Vince论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Gainesville, FL USA Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USABoye, Sanford L.论文数: 0 引用数: 0 h-index: 0机构: Univ Florida, Coll Med, Gainesville, FL USA Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USAGuy, John论文数: 0 引用数: 0 h-index: 0机构: Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USA Univ Miami, Miller Sch Med, Bascom Palmer Eye Inst, Miami, FL 33136 USA
- [43] Efficacy Evaluation of EXG102-031, A Novel AAV-based Gene Therapy for Neovascular AMD in a Mouse Model of VEGF-A-induced Exudative Retinal Detachment vascular leakage Mouse ModelINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2023, 64 (08)Ye, Guojie论文数: 0 引用数: 0 h-index: 0机构: Exegenesis Bio, Lower Gwynedd Township, PA USA Exegenesis Bio, Lower Gwynedd Township, PA USAShen, Jikui论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Exegenesis Bio, Lower Gwynedd Township, PA USADai, Li论文数: 0 引用数: 0 h-index: 0机构: Exegenesis Bio, Lower Gwynedd Township, PA USA Exegenesis Bio, Lower Gwynedd Township, PA USAFormica, Raquel论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Exegenesis Bio, Lower Gwynedd Township, PA USAWang, Lijun论文数: 0 引用数: 0 h-index: 0机构: Exegenesis Bio, Lower Gwynedd Township, PA USA Exegenesis Bio, Lower Gwynedd Township, PA USAWu, Zhenhua论文数: 0 引用数: 0 h-index: 0机构: Exegenesis Bio, Lower Gwynedd Township, PA USA Exegenesis Bio, Lower Gwynedd Township, PA USACampochiaro, Peter A.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Exegenesis Bio, Lower Gwynedd Township, PA USA
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- [45] A GLP-Compliant Toxicology and Biodistribution Study of ADVM-062 (AAV.7m8-L-opsin), a Novel Gene Therapy Product Being Developed as a Potential Single Intravitreal Administration for the Treatment of Blue Cone MonochromacyMOLECULAR THERAPY, 2022, 30 (04) : 589 - 589Hanna, Kelly论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USAEngbers, Charles论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USANieves, Julio论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USASharma, Pallavi论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USABender, Kristina Oresic论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USARenz, Mark论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USAYu, Joseph论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USATai, Alex论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USADuncan, Scott论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USASzeto, May论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USAJouttijarvi, Heikki论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USACepeda, Diana论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USAGelfman, Claire论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USARiley, Brigit E.论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USAGrishanin, Ruslan论文数: 0 引用数: 0 h-index: 0机构: Adverum Biotechnol, Redwood City, CA USA Adverum Biotechnol, Redwood City, CA USA
- [46] Novel Engineered Cardiac-Specific AAV Vectors via Directed Molecular-Evolution in Human-Relevant Model Systems Outperform Current Benchmark Vectors for Clinical Cardiac Gene TherapyMOLECULAR THERAPY, 2024, 32 (04) : 256 - 256Habeck, Gregor论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanySchweiggert, Joerg论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanySmuglov, Michael论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyFerdinand, Johanna论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyKehr, Dorothea论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyCimen, Kristin论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyKramp, Xenia论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyKatus, Hugo A.论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyLerchenmueller, Marc Johannes论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyMietsch, Matthias论文数: 0 引用数: 0 h-index: 0机构: German Primate Ctr, Gottingen, Germany AaviGen GmbH, Heidelberg, GermanyErffmeier, Lena论文数: 0 引用数: 0 h-index: 0机构: German Primate Ctr, Gottingen, Germany AaviGen GmbH, Heidelberg, GermanyHinkel, Rabea论文数: 0 引用数: 0 h-index: 0机构: German Primate Ctr, Gottingen, Germany AaviGen GmbH, Heidelberg, GermanyMost, Patrick论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, GermanyBusch, Martin论文数: 0 引用数: 0 h-index: 0机构: AaviGen GmbH, Heidelberg, Germany AaviGen GmbH, Heidelberg, Germany
- [47] Treatment of SMA type 1 infants using a single-dose AAV9-mediated gene therapy via intrathecal injection of GC101: An open-label, single-arm study中华医学杂志英文版, 2024, 137 (16)Ma Xiuwei论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhuang Lu论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaMa Wenhao论文数: 0 引用数: 0 h-index: 0机构: Research and Development Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaLi Jun论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaWang Xiaodong论文数: 0 引用数: 0 h-index: 0机构: Medical Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaLi Zhongqiu论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaJiang Xinyang论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaWang Yongxia论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaDu Ying论文数: 0 引用数: 0 h-index: 0机构: Medical Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhang Yingqian论文数: 0 引用数: 0 h-index: 0机构: Medical Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaHe Fang论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhu Zhiming论文数: 0 引用数: 0 h-index: 0机构: Medical Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaDu Shaopeng论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaXu Juan论文数: 0 引用数: 0 h-index: 0机构: Department of Pharmacy, Medical Supplies Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaGu Ruijie论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhang Yanping论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhang Shan论文数: 0 引用数: 0 h-index: 0机构: Beijing Key Laboratory of Pediatric Organ Failure, Beijing, Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaLi Ting论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaYang Xiao论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhang Sheng论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaZhu Lina论文数: 0 引用数: 0 h-index: 0机构: National Engineering Laboratory for Birth Defects Prevention and Control of Key Technology, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaLi Qiuping论文数: 0 引用数: 0 h-index: 0机构: Beijing Key Laboratory of Pediatric Organ Failure, Beijing, Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaDong Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Medical Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaWu Xiaobing论文数: 0 引用数: 0 h-index: 0机构: Research and Development Division, Genecradle Therapeutics Inc, Beijing, China Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, ChinaFeng Zhichun论文数: 0 引用数: 0 h-index: 0机构: Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China Beijing Key Laboratory of Pediatric Organ Failure, Beijing, Department of Neurodevelopment, Faculty of Pediatrics, The Seventh Medical Center of Chinese PLA General Hospital, Beijing, China
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100700, Peoples R ChinaLi, Jun论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaWang, Xiaodong论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Med Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaLi, Zhongqiu论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaJiang, Xinyang论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaWang, Yongxia论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaDu, Ying论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Med Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhang, Yingqian论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Med Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaHe, Fang论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhu, Zhiming论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Med Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaDu, Shaopeng论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaXu, Juan论文数: 0 引用数: 0 h-index: 0机构: China PLA Gen Hosp, Med Care Ctr, Dept Pharm, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaGu, Ruijie论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhang, Yanping论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhang, Shan论文数: 0 引用数: 0 h-index: 0机构: Beijing Key Lab Pediat Organ Failure, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaLi, Ting论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaYang, Xiao论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhang, Sheng论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaZhu, Lina论文数: 0 引用数: 0 h-index: 0机构: Natl Engn Lab Birth Defects Prevent & Control Key, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaLi, Qiuping论文数: 0 引用数: 0 h-index: 0机构: Beijing Key Lab Pediat Organ Failure, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaDong, Xiaoyan论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Med Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaWu, Xiaobing论文数: 0 引用数: 0 h-index: 0机构: Genecradle Therapeut Inc, Res & Dev Div, Beijing 100176, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R ChinaFeng, Zhichun论文数: 0 引用数: 0 h-index: 0机构: Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China Beijing Key Lab Pediat Organ Failure, Beijing 100700, Peoples R China Chinese Peoples Liberat Army Gen Hosp, Fac Pediat, Med Ctr 7, Dept Neurodev, Beijing 100700, Peoples R China
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- [50] Relevance of NHP safety studies for ocular delivery of AAV-based gene therapy in humans: Example of GS010 (rAAV2/2-ND4) local tolerability, shedding and immunogenicity for the treatment of Leber Hereditary Optic Neuropathy (LHON), after intravitreal (IVT) injection in non-human primates (NHP) and in LHON patientsINVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2015, 56 (07)Thomasson, Nitza论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceGaly, Anne论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceFitoussi, Serge论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceMeunier, Sandrine论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceUretsky, Scott论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, FranceCombal, Jean-Philippe论文数: 0 引用数: 0 h-index: 0机构: GenSight Biol, Paris, France GenSight Biol, Paris, France