Discovering A Novel AAV Variant for Efficient RPE Transfection via Intravitreal Injection for Dry AMD Gene Therapy

被引:0
|
作者
Singh, Sonali [1 ]
Visel, Meike [2 ]
Byrne, Leah [2 ,3 ]
Ozturk, Bilge Esin [4 ]
Rickman, Catherine Bowes [5 ]
Flannery, John Gerard [1 ]
机构
[1] Univ Calif Berkeley, Vis Sci, Berkeley, CA 94720 USA
[2] Univ Calif Berkeley, Helen Wills Dept Neurosci, Berkeley, CA 94720 USA
[3] Univ Pittsburgh, Dept Ophthalmol, Pittsburgh, PA 15260 USA
[4] MeiraGTx HIdgs, London, England
[5] Duke Univ, Dept Ophthalmol, Durham, NC USA
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R77 [眼科学];
学科分类号
100212 ;
摘要
5328
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页数:3
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