Gene therapy for Wnt signalling-related retinal detachment: Intravitreal injection of AAV.NDP is an effective treatment for vascular exudation in a mouse model of familial exudative vitreoretinopathy (FEVR)/ Coats disease

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作者
Wawrzynski, James [1 ,2 ]
Henderson, Robert [2 ,3 ]
Pauzuolyte, Valda [1 ]
Patel, Aara [1 ,2 ]
Coombe-Tennant, Oliver [1 ]
Moulding, Dale [1 ]
Sowden, Jane C. [1 ]
机构
[1] UCL, Inst Child Hlth, London, England
[2] Great Ormond St Hosp Children NHS Fdn Trust, London, England
[3] Moorfields Eye Hosp NHS Fdn Trust, London, England
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R77 [眼科学];
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100212 ;
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页数:3
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