Preclinical Safety and Efficacy of Intein-Based Dual-AAV Gene Therapy for Stargardt Disease

被引：0
|
作者：
Vila-Perello, Miquel [1 ]
Di Scala, Marianna [1 ]
Aisa, Izarbe [1 ]
Abad, Victor [1 ]
Caelles, Gerard [1 ]
Esteve Rudd, Julian [1 ]
Frutos, Silvia [1 ]
Favre, David [1 ]
机构：
[1] SpliceBio, Barcelona, Spain
来源：
MOLECULAR THERAPY | 2024年 / 32卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
655
引用
收藏
页码：333 / 333
页数：1
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