Preclinical Safety and Efficacy of Intein-Based Dual-AAV Gene Therapy for Stargardt Disease

被引：0

作者：

Vila-Perello, Miquel ^{[1
]}

Di Scala, Marianna ^{[1
]}

Aisa, Izarbe ^{[1
]}

Abad, Victor ^{[1
]}

Caelles, Gerard ^{[1
]}

Esteve Rudd, Julian ^{[1
]}

Frutos, Silvia ^{[1
]}

Favre, David ^{[1
]}

机构：

[1] SpliceBio, Barcelona, Spain

来源：

MOLECULAR THERAPY | 2024年 / 32卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

655

引用

页码：333 / 333

页数：1

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