共 50 条
- [42] Gene therapy of metachromatic leukodystrophy by AAV vectors JOURNAL OF GENE MEDICINE, 2006, 8 (03): : 393 - 393
- [43] AAV vectors for hemophilia B gene therapy MOUNT SINAI JOURNAL OF MEDICINE, 2004, 71 (05): : 305 - 313
- [46] AAV vectors for gene therapy of retinal degeneration HUMAN GENE THERAPY, 2010, 21 (10) : 1393 - 1393