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机构:
Univ Massachusetts, Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA
Univ Massachusetts, Med Sch, Li Weibo Inst Rare Dis Res, Worcester, MA 01605 USA
Univ Massachusetts, Med Sch, Dept Microbiol & Physiol Syst, Worcester, MA 01605 USA Univ Miami, Miller Sch Med, Dept Pathol, Miami, FL 33136 USA