TREATMENT OF PATIENTS WITH SEVERE COMBINED IMMUNODEFICIENCY DUE TO ADENOSINE-DEAMINASE (ADA) DEFICIENCY BY AUTOLOGOUS TRANSPLANTATION OF GENETICALLY MODIFIED BONE-MARROW CELLS

被引：27
|
作者：
HOOGERBRUGGE, PM [1 ]
VOSSEN, JMJJ [1 ]
VONBEUSECHEM, VW [1 ]
VALERIO, D [1 ]
机构：
[1] TNO,INST APPL RADIOBIOL & IMMUNOL,DEPT GENE THERAPY,2280 HV RIJSWIJK,NETHERLANDS
来源：
HUMAN GENE THERAPY | 1992年 / 3卷 / 05期
关键词：
D O I：
10.1089/hum.1992.3.5-553
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
[No abstract available]
引用
收藏
页码：553 / 558
页数：6
相关论文
共 50 条
  • [31] ADENOSINE-DEAMINASE ACTIVITY IN NORMAL TISSUES AND TISSUES FROM A CHILD WITH SEVERE COMBINED IMMUNODEFICIENCY AND ADENOSINE-DEAMINASE DEFICIENCY
    HIRSCHHORN, R
    MARTINIUK, F
    ROSEN, FS
    CLINICAL IMMUNOLOGY AND IMMUNOPATHOLOGY, 1978, 9 (03): : 287 - 292
  • [32] ENZYME REPLACEMENT THERAPY FOR ADENOSINE-DEAMINASE DEFICIENCY AND SEVERE COMBINED IMMUNODEFICIENCY
    POLMAR, SH
    STERN, RC
    SCHWARTZ, AL
    WETZLER, EM
    CHASE, PA
    HIRSCHHORN, R
    NEW ENGLAND JOURNAL OF MEDICINE, 1976, 295 (24): : 1337 - 1343
  • [33] METABOLIC FINDINGS IN A PATIENT WITH ADENOSINE-DEAMINASE DEFICIENCY AND SEVERE COMBINED IMMUNODEFICIENCY
    CARAPELLADELUCA, E
    STEGAGNO, M
    LUCARELLI, P
    SIGNORETTI, A
    IMPERATO, C
    WADMAN, SK
    LEYVA, A
    ASTALDI, A
    ADVANCES IN EXPERIMENTAL MEDICINE AND BIOLOGY, 1984, 165 : 159 - 162
  • [34] LYMPHOMA IN A PATIENT WITH SEVERE COMBINED IMMUNODEFICIENCY WITH ADENOSINE-DEAMINASE DEFICIENCY, FOLLOWING UNSUSTAINED ENGRAFTMENT OF HISTOINCOMPATIBLE T-CELL-DEPLETED BONE-MARROW
    KAPOOR, N
    JUNG, LKL
    ENGELHARD, D
    FILLER, J
    SHALIT, I
    LANDRETH, KS
    GOOD, RA
    JOURNAL OF PEDIATRICS, 1986, 108 (03): : 435 - 438
  • [35] HETEROGENEITY OF BIOCHEMICAL, CLINICAL AND IMMUNOLOGICAL PARAMETERS IN SEVERE COMBINED IMMUNODEFICIENCY DUE TO ADENOSINE-DEAMINASE DEFICIENCY
    MORGAN, G
    LEVINSKY, RJ
    HUGHJONES, K
    FAIRBANKS, LD
    MORRIS, GS
    SIMMONDS, HA
    CLINICAL AND EXPERIMENTAL IMMUNOLOGY, 1987, 70 (03): : 491 - 499
  • [36] PURINE NUCLEOSIDE METABOLISM IN ERYTHROCYTES OF PATIENTS WITH ADENOSINE-DEAMINASE DEFICIENCY AND SEVERE COMBINED IMMUNODEFICIENCY
    AGARWAL, RP
    CRABTREE, GW
    PARKS, RE
    NELSON, JA
    KEIGHTLEY, R
    PARKMAN, R
    ROSEN, FS
    STERN, RC
    POLMAR, SH
    JOURNAL OF CLINICAL INVESTIGATION, 1976, 57 (04): : 1025 - 1035
  • [37] RECONSTITUTION OF T-CELL AND B-CELL FUNCTION AFTER LYMPHOCYTE-T-DEPLETED HAPLOIDENTICAL BONE-MARROW TRANSPLANTATION IN SEVERE COMBINED IMMUNODEFICIENCY DUE TO ADENOSINE-DEAMINASE DEFICIENCY
    SILBER, GM
    WINKELSTEIN, JA
    MOEN, RC
    HOROWITZ, SD
    TRIGG, M
    HONG, R
    CLINICAL IMMUNOLOGY AND IMMUNOPATHOLOGY, 1987, 44 (03): : 317 - 320
  • [38] HOMOZYGOSITY FOR A NEWLY IDENTIFIED MISSENSE MUTATION IN A PATIENT WITH VERY SEVERE COMBINED IMMUNODEFICIENCY DUE TO ADENOSINE-DEAMINASE DEFICIENCY (ADA-SCID)
    HIRSCHHORN, R
    CHAKRAVARTI, V
    PUCK, J
    DOUGLAS, SD
    AMERICAN JOURNAL OF HUMAN GENETICS, 1991, 49 (04) : 878 - 885
  • [39] BONE-MARROW TRANSPLANTATION IN SEVERE COMBINED IMMUNODEFICIENCY
    KOCH, C
    HENRIKSEN, K
    JUHL, F
    ANDERSEN, V
    DUPONT, B
    FABER, V
    JENSEN, K
    MULLERBE.N
    SVEJGAARD, A
    UTZON, F
    SCANDINAVIAN JOURNAL OF IMMUNOLOGY, 1973, 2 (03) : 320 - 320
  • [40] ENZYME REPLACEMENT THERAPY FOR ADENOSINE-DEAMINASE DEFICIENCY AND SEVERE COMBINED IMMUNODEFICIENCY DISEASE
    POLMAR, SH
    STERN, RC
    SCHWARTZ, AL
    HIRSCHHORN, R
    PEDIATRIC RESEARCH, 1976, 10 (04) : 392 - 392
12345