ENZYME REPLACEMENT THERAPY IN FELINE MUCOPOLYSACCHARIDOSIS-I (MPS-I)

被引:0
|
作者
HASKINS, ME
KAKKIS, ED
WAN, Q
WEIL, MA
AGUIRRE, GD
SCHUCHMAN, EH
机构
[1] UNIV CALIF LOS ANGELES,HARBOR MED CTR,LOS ANGELES,CA 90024
[2] UNIV PENN,PHILADELPHIA,PA 19104
[3] MT SINAI SCH MED,NEW YORK,NY
[4] CORNELL UNIV,ITHACA,NY
关键词
D O I
暂无
中图分类号
Q3 [遗传学];
学科分类号
071007 ; 090102 ;
摘要
引用
收藏
页码:194 / 194
页数:1
相关论文
共 50 条
  • [31] Induction of immune tolerance to enzyme replacement therapy in mucopolysaccharidosis type I
    Liao, Ai Yin
    Ghosh, Arunabha
    O'Leary, Claire
    Mercer, Jean
    Church, Heather J.
    Tylee, Karen L.
    Goenka, Anu
    Holley, Rebecca
    Wynn, Robert F.
    Jones, Simon A.
    Bigger, Brian W.
    MOLECULAR GENETICS AND METABOLISM, 2018, 123 (02) : S86 - S86
  • [32] Enzyme replacement therapy with laronidase (Aldurazyme®) for treating mucopolysaccharidosis type I
    Jameson, E.
    Jones, S.
    Remmington, T.
    COCHRANE DATABASE OF SYSTEMATIC REVIEWS, 2019, (06):
  • [33] Mucopolysaccharidosis type I: the youngest patient to be treated with enzyme replacement therapy
    Mercanti, F.
    Tomassetti, S.
    Caponi, L.
    Di Tondo, E.
    D'Ascenzo, R.
    Santoro, L.
    Petroni, V.
    Ficcadenti, A.
    ACTA PAEDIATRICA, 2008, 97 : 104 - 105
  • [34] Synergistic effects of resveratrol and enzyme replacement therapy in the Mucopolysaccharidosis type I
    Rintz, Estera
    Ziemian, Maja
    Kobus, Barbara
    Gaffke, Lidia
    Pierzynowska, Karolina
    Wegrzyn, Grzegorz
    BIOCHEMICAL PHARMACOLOGY, 2024, 229
  • [35] Enzyme replacement therapy for MPS I: When is the right time to stop?
    Berry, Lisa
    Bailey, Laurie
    Leslie, Nancy
    MOLECULAR GENETICS AND METABOLISM, 2013, 108 (02) : S24 - S24
  • [36] Cardiomyopathy and reduced volume enzyme replacement therapy in patients with MPS I
    Grant, Christina L.
    Kuperman, KeriAnn W.
    Failla, Allison
    MOLECULAR GENETICS AND METABOLISM, 2025, 144 (02)
  • [37] Observation of oral communication changes and oral miofunctional changes in 9 Brazilian mucopolysaccharidosis type I (MPS I) patients on enzyme replacement therapy (ERT)
    Mello, I. M. Z.
    Guedes, Z. F. C.
    Micheletti, C.
    Secches, T. A. V. A.
    Kyosen, S. O.
    Martins, A. M.
    JOURNAL OF INHERITED METABOLIC DISEASE, 2006, 29 : 151 - 151
  • [38] ALLELISM AND GENETIC COMPOUNDS AT MPS-I LOCUS
    MAUMENEE, IH
    KELLY, TE
    MCKUSICK, VA
    AMERICAN JOURNAL OF HUMAN GENETICS, 1975, 27 (06) : A64 - A64
  • [39] Liver-Directed Gene Therapy for Mucopolysaccharidosis Type I (MPS I)
    Gurda, Brittney
    Bell, Peter
    Zhu, Yanqing
    Wang, Ping
    O'Donnell, Patty
    Sanmiguel, Julio
    Vandenberghe, Luk
    Haskins, Mark
    Wilson, James
    MOLECULAR GENETICS AND METABOLISM, 2012, 105 (02) : S32 - S32
  • [40] Aldurazyme® (laronidase) enzyme replacement therapy for mucopolysaccharidosis I:: A dose optimization study
    Cox, G. E.
    Giugliani, R.
    Martins, A. M.
    Valadares, E. R.
    Clarke, J. T. R.
    Goes, J. E. C.
    Worden, M. A.
    Sidman, M.
    Kakkis, E. D.
    CLINICAL THERAPEUTICS, 2007, 29 : S125 - S126