CORRECTION OF ADENOSINE-DEAMINASE DEFICIENCY IN CULTURED HUMAN T-CELLS AND B-CELLS BY RETROVIRUS-MEDIATED GENE-TRANSFER

被引:165
|
作者
KANTOFF, PW
KOHN, DB
MITSUYA, H
ARMENTANO, D
SIEBERG, M
ZWIEBEL, JA
EGLITIS, MA
MCLACHLIN, JR
WIGINTON, DA
HUTTON, JJ
HOROWITZ, SD
GILBOA, E
BLAESE, RM
ANDERSON, WF
机构
[1] NCI,METAB BRANCH,BETHESDA,MD 20892
[2] NCI,CLIN ONCOL PROGRAM,BETHESDA,MD 20892
[3] PRINCETON UNIV,DEPT MOLEC BIOL,PRINCETON,NJ 08544
[4] UNIV CINCINNATI,CHILDRENS HOSP MED CTR,DEPT PEDIAT,CINCINNATI,OH 45229
[5] UNIV WISCONSIN HOSP,DEPT PEDIAT,MADISON,WI 53792
关键词
D O I
10.1073/pnas.83.17.6563
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:6563 / 6567
页数:5
相关论文
共 50 条
  • [31] HUMAN PURINE NUCLEOSIDE PHOSPHORYLASE AND ADENOSINE-DEAMINASE - GENE-TRANSFER INTO CULTURED-CELLS AND MURINE HEMATOPOIETIC STEM-CELLS BY USING RECOMBINANT AMPHOTROPIC RETROVIRUSES
    MCIVOR, RS
    JOHNSON, MJ
    MILLER, AD
    PITTS, S
    WILLIAMS, SR
    VALERIO, D
    MARTIN, DW
    VERMA, IM
    MOLECULAR AND CELLULAR BIOLOGY, 1987, 7 (02) : 838 - 846
  • [32] THE HEMATOPOIETIC STROMAL MICROENVIRONMENT PROMOTES RETROVIRUS-MEDIATED GENE-TRANSFER INTO HEMATOPOIETIC STEM-CELLS
    CHERTKOV, JL
    JIANG, S
    LUTTON, JD
    HARRISON, J
    LEVERE, RD
    TIEFENTHALER, M
    ABRAHAM, NG
    STEM CELLS, 1993, 11 (03) : 218 - 227
  • [33] Retrovirus-mediated correction of the metabolic defect in cultured Farber disease cells
    Medin, JA
    Takenaka, T
    Carpentier, S
    Garcia, V
    Basile, JP
    Segui, B
    Andrieu-Abadie, N
    Auge, N
    Salvayre, R
    Levade, T
    HUMAN GENE THERAPY, 1999, 10 (08) : 1321 - 1329
  • [34] EFFECTS OF DEOXYRIBONUCLEOSIDES ON HUMAN LYMPHOBLASTOID B AND T CELLS - MODEL FOR NUCLEOSIDE PHOSPHORYLASE AND ADENOSINE-DEAMINASE DEFICIENCY
    OCHS, UH
    CHEN, SH
    OCHS, HD
    SCOTT, CR
    FEDERATION PROCEEDINGS, 1979, 38 (03) : 1222 - 1222
  • [35] RETROVIRUS-MEDIATED GENE-TRANSFER OF THE HUMAN GAMMA-IFN GENE - A THERAPY FOR CANCER
    HOWARD, B
    BURRASCANO, M
    MCCALLISTER, T
    CHONG, K
    GANGAVALLI, R
    SEVERINSSON, L
    JOLLY, DJ
    DARROW, T
    VERVAERT, C
    ABDELWAHAB, Z
    SIEGLER, HF
    BARBER, JR
    GENE THERAPY FOR NEOPLASTIC DISEASES, 1994, 716 : 167 - 187
  • [36] THE HEMATOPOIETIC STROMAL MICROENVIRONMENT PROMOTES RETROVIRUS-MEDIATED GENE-TRANSFER INTO HEMATOPOIETIC STEM-CELLS
    JIANG, SL
    LUTTON, JD
    HARRISON, J
    ABRAHAM, NG
    EXPERIMENTAL HEMATOLOGY, 1993, 21 (05) : 725 - 725
  • [37] PREPARATION OF ADENOSINE-DEAMINASE (ADA) CORRECTED T-CELLS FOR USE IN GENE-THERAPY
    CARTER, CS
    GUTIERREZ, RH
    MAY, FF
    YU, MY
    LEITMAN, SF
    KLEIN, HG
    CHANG, L
    ANDERSON, WF
    CULVER, KW
    BLAESE, RM
    TRANSFUSION, 1992, 32 (08) : S46 - S46
  • [38] RETROVIRUS MEDIATED GENE-TRANSFER INTO HEMATOPOIETIC-CELLS
    VONMELCHNER, H
    HOFFKEN, K
    BLUT, 1988, 57 (01): : 1 - 5
  • [39] RETROVIRUS-MEDIATED GENE-TRANSFER OF HUMAN PYRUVATE-KINASE (PK) CDNA INTO MURINE HEMATOPOIETIC-CELLS - IMPLICATIONS FOR GENE-THERAPY OF HUMAN PK DEFICIENCY
    TANI, K
    YOSHIKUBO, T
    IKEBUCHI, K
    TAKAHASHI, K
    TSUCHIYA, T
    TAKAHASHI, S
    SHIMANE, M
    OGURA, H
    TOJO, A
    OZAWA, K
    TAKAHARA, Y
    NAKAUCHI, H
    MARKOWITZ, D
    BANK, A
    ASANO, S
    BLOOD, 1994, 83 (08) : 2305 - 2310
  • [40] Amelioration of retrovirus-mediated gene transfer into hepatocellular carcinoma cells
    Tsujinoue, H
    Kuriyama, S
    Nakatani, T
    Yoshiji, H
    Akahane, T
    Toyokawa, Y
    Fukui, H
    Yoshimatsu, T
    Ikenaka, K
    INTERNATIONAL JOURNAL OF ONCOLOGY, 2001, 18 (04) : 801 - 807