REPLACEMENT THERAPY FOR INHERITED ENZYME DEFICIENCY - USE OF PURIFIED GLUCOCEREBROSIDASE IN GAUCHERS-DISEASE

被引：233
|
作者：
BRADY, RO [1 ]
PENTCHEV, PG [1 ]
GAL, AE [1 ]
HIBBERT, SR [1 ]
DEKABAN, AS [1 ]
机构：
[1] NINDS,DEV & METAB NEUROL BRANCH,BLDG 10,RM 3003,BETHESDA,MD 20014
来源：
NEW ENGLAND JOURNAL OF MEDICINE | 1974年 / 291卷 / 19期
关键词：
D O I：
10.1056/NEJM197411072911901
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：989 / 993
页数：5
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