The total number of rare conditions is debated, partly because of the variety of definitions of what constitutes rare. A broader consensus view of what rare means, based on improved understanding of individual group and patient clinicopathological characteristics, will help maximize the impact of technological advances in therapeutic development programmes.
机构:
Chinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
Univ Chinese Acad Sci, Beijing 100049, Peoples R ChinaChinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
Huang, Min
Geng, Mei-yu
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Chinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
Univ Chinese Acad Sci, Beijing 100049, Peoples R ChinaChinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
Geng, Mei-yu
Ding, Jian
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Chinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
Univ Chinese Acad Sci, Beijing 100049, Peoples R ChinaChinese Acad Sci, Shanghai Inst Mat Med, State Key Lab Drug Res, Shanghai 201203, Peoples R China
机构:
Mem Sloan Kettering Canc Ctr, Dept Pathol, 1275 York Ave, New York, NY 10021 USAMem Sloan Kettering Canc Ctr, Dept Pathol, 1275 York Ave, New York, NY 10021 USA
Durham, Benjamin H.
Diamond, Eli L.
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Mem Sloan Kettering Canc Ctr, Dept Neurol, 1275 York Ave, New York, NY 10021 USAMem Sloan Kettering Canc Ctr, Dept Pathol, 1275 York Ave, New York, NY 10021 USA
Diamond, Eli L.
Abdel-Wahab, Omar
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Mem Sloan Kettering Canc Ctr, Human Oncol & Pathogenesis Program, 1275 York Ave, New York, NY 10021 USA
Mem Sloan Kettering Canc Ctr, Dept Med, Leukemia Serv, 1275 York Ave, New York, NY 10021 USAMem Sloan Kettering Canc Ctr, Dept Pathol, 1275 York Ave, New York, NY 10021 USA
机构:
Ohio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Bumma, Naresh
Kahwash, Rami
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Ohio State Univ, Dept Internal Med, Div Cardiol, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Kahwash, Rami
Parikh, Samir V.
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Ohio State Univ, Dept Internal Med, Div Nephrol, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Parikh, Samir V.
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Isfort, Michael
Freimer, Miriam
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Ohio State Univ, Dept Neurol, Div Neuromuscular Med, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Freimer, Miriam
Vallakati, Ajay
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Ohio State Univ, Dept Internal Med, Div Cardiol, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Vallakati, Ajay
Redder, Elyse
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Ohio State Univ, Oncol Rehabil, James Canc Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Redder, Elyse
Campbell, Courtney M.
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Ohio State Univ, Dept Internal Med, Div Cardiol, Wexner Med Ctr, Columbus, OH USA
Washington Univ, Cardiooncol Ctr Excellence, Cardiovasc Div, St Louis, MO USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Campbell, Courtney M.
Sharma, Nidhi
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Ohio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Sharma, Nidhi
Efebera, Yvonne
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机构:
Ohio Hlth, Dept Hematol Oncol & Blood & Marrow Transplant, Columbus, OH USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
Efebera, Yvonne
Stino, Amro
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Univ Michigan, Dept Neurol, Div Neuromuscular Med, Med Sch, Ann Arbor, MI 48103 USAOhio State Univ, Dept Internal Med, Div Hematol Oncol, Wexner Med Ctr, Columbus, OH USA
机构:
Univ Michigan, Dept Internal Med, Div Hematol Oncol, Ann Arbor, MI 48109 USAUniv Michigan, Dept Internal Med, Div Hematol Oncol, Ann Arbor, MI 48109 USA