Gene editing for Duchenne muscular dystrophy

被引：0
|
作者：
Hannah Stower
机构：
[1] Nature Medicine,
来源：
Nature Medicine | 2018年 / 24卷
关键词：
D O I：
暂无
中图分类号：
学科分类号：
摘要：
引用
收藏
页码：1491 / 1491
相关论文
共 50 条
  • [41] The FDA and Gene Therapy for Duchenne Muscular Dystrophy
    Rind, David M.
    JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2024, 331 (20): : 1705 - 1706
  • [42] Advances in Duchenne muscular dystrophy gene therapy
    van Deutekom, JCT
    van Ommen, GJB
    NATURE REVIEWS GENETICS, 2003, 4 (10) : 774 - 783
  • [43] Modeling Gene Editing Outcomes in Microphysiological Human Tissue System Models of Duchenne Muscular Dystrophy
    Sitton, Madeleine J.
    Khodabukus, Alastair
    Bohning, Joel D.
    Bursac, Nenad
    Gersbach, Charles A.
    MOLECULAR THERAPY, 2023, 31 (04) : 65 - 65
  • [44] Preclinical Development of MyoDys45-55, a Gene Editing Therapy for Duchenne Muscular Dystrophy
    Dorst, William
    Gibbs, Elizabeth
    Nguyen, Jonathan
    Perez, Jesus
    Hagerty, Laura
    Emami, Michael R.
    Bengtsson, Niclas E.
    Chamberlain, Jeffrey S.
    Pyle, April D.
    Spencer, Melissa J.
    Young, Courtney S.
    MOLECULAR THERAPY, 2023, 31 (04) : 332 - 332
  • [45] Ex Vivo Gene Therapy of Duchenne Muscular Dystrophy Using iPSCs from Duchenne Muscular Dystrophy Patients
    Maltais, Chantale
    Gravel, William-Edouard
    Lebel, Carl
    Tremblay, Jacques P.
    MOLECULAR THERAPY, 2014, 22 : S56 - S56
  • [46] Genome editing shows promise in an in vivo model of Duchenne muscular dystrophy
    Heather Wood
    Nature Reviews Neurology, 2016, 12 (2) : 63 - 63
  • [47] Restoration of dystrophin expression and correction of Duchenne muscular dystrophy by genome editing
    Aslesh, Tejal
    Erkut, Esra
    Yokota, Toshifumi
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2021, 21 (08) : 1049 - 1061
  • [48] Duchenne muscular dystrophy: genome editing gives new hope for treatment
    Crispi, Vassili
    Matsakas, Antonios
    POSTGRADUATE MEDICAL JOURNAL, 2018, 94 (1111) : 296 - 304
  • [49] GENOME EDITING THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY-ASSOCIATED CARDIOMYOPATHY
    Xu, L.
    Lau, Y.
    Gao, Y.
    Ma, J.
    Han, R.
    CARDIOLOGY, 2018, 140 : 384 - 384
  • [50] Becker muscular dystrophy: a natural gene editing
    Perez, I.
    Sabater, M.
    Nicolas, M. E.
    Martinez, M. C.
    Olmo, M. C.
    Lopez, D.
    Gil, C.
    Glover, G.
    Gimeno, J. R.
    EUROPEAN JOURNAL OF HUMAN GENETICS, 2018, 26 : 428 - 428
12345