共 50 条
- [34] AAV9 Vector: a Novel modality in gene therapy for spinal muscular atrophy Gene Therapy, 2019, 26 : 287 - 295
- [35] Gene therapy rescues newborns with spinal muscular atrophy Nature Biotechnology, 2018, 36 : 669 - 670
- [37] New Routes to Therapy for Spinal and Bulbar Muscular Atrophy Journal of Molecular Neuroscience, 2013, 50 : 514 - 523
- [38] Cell-Based Therapy for Spinal Muscular Atrophy STEM CELL-BASED THERAPY FOR NEURODEGENERATIVE DISEASES, 2020, 1266 : 117 - 125
- [40] Gene therapy for spinal muscular atrophy: hope and caution LANCET NEUROLOGY, 2021, 20 (04): : 251 - +