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- [41] Correction of the Marfan Syndrome Pathogenic FBN1 Mutation by Base Editing in Human Cells and Heterozygous EmbryosMOLECULAR THERAPY, 2018, 26 (11) : 2631 - 2637Zeng, Yanting论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China论文数: 引用数: h-index:机构:Li, Guanglei论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaHuang, Shisheng论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Sch Life Sci & Technol, 100 Haike Rd, Shanghai 201210, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaYu, Wenxia论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Sch Life Sci & Technol, 100 Haike Rd, Shanghai 201210, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaZhang, Yu论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Sch Life Sci & Technol, 100 Haike Rd, Shanghai 201210, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaChen, Dunjin论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Key Lab Major Obstet Dis Guangdong Prov, Key Lab Reprod & Genet,Guangdong Higher Educ Inst, Guangzhou 510150, Guangdong, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaChen, Jia论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Sch Life Sci & Technol, 100 Haike Rd, Shanghai 201210, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaLiu, Jianqiao论文数: 0 引用数: 0 h-index: 0机构: Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R ChinaHuang, Xingxu论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Sch Life Sci & Technol, 100 Haike Rd, Shanghai 201210, Peoples R China Chinese Acad Sci, Univ Chinese Acad Sci, Shanghai Inst Biochem & Cell Biol, CAS Ctr Excellence Mol Cell Sci, 320 Yueyang Rd, Shanghai 200031, Peoples R China Guangzhou Med Univ, Affiliated Hosp 3, Dept Reprod Med, 63 Duobao Rd, Guangzhou 510150, Guangdong, Peoples R China
- [42] Publisher Correction: Whole Transcriptome Analysis of Renal Intercalated Cells Predicts Lipopolysaccharide Mediated Inhibition of Retinoid X Receptor alpha FunctionScientific Reports, 10Vijay Saxena论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineJames Fitch论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineJohn Ketz论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicinePeter White论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineAmy Wetzel论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineMelinda A. Chanley论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineJohn D. Spencer论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineBrian Becknell论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineKeith R. Pierce论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineSam W. Arregui论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineRaoul D. Nelson论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineGeorge J. Schwartz论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineVictoria Velazquez论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineLogan A. Walker论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineXi Chen论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicinePearlly Yan论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineDavid S. Hains论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of MedicineAndrew L. Schwaderer论文数: 0 引用数: 0 h-index: 0机构: Riley Children’s Hospital,Indiana University School of Medicine
- [43] ENHANCED MITOCHONDRIAL BASE EDITING SYSTEM FOR NEAR COMPLETE MITOCHONDRIAL GENOME EDITING IN HUMAN PRIMARY CELLS SUITABLE FOR DISEASE MODELING AND FOR POTENTIAL THERAPEUTIC APPLICATIONSCYTOTHERAPY, 2023, 25 (06) : S25 - S25Kar, B.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USAThulung, L. Rai论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USACastillo, S. R.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USASabharwal, A.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USAClark, K.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USAEkker, S.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA Mayo Clin Minnesota, Dept Biochem & Mol Biol, Rochester, MN USA
- [44] Precision Medicine in Cardiac Channelopathy: Integrating Genome Editing and Induced Pluripotent Stem Cells to Decipher Variant of Unknown SignificanceCIRCULATION RESEARCH, 2018, 123Garg, Priyanka论文数: 0 引用数: 0 h-index: 0
- [45] KPT330 improves Cas9 precision genome- and base-editing by selectively regulating mRNA nuclear exportCOMMUNICATIONS BIOLOGY, 2022, 5 (01)Cui, Yan-ru论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaWang, Shao-jie论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaMa, Tiancheng论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Ctr Excellence Mol Synth, Shanghai Inst Organ Chem, Key Lab Organofluorine Chem, 345 Ling Ling Rd, Shanghai 200032, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaYu, Peihong论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Univ Chinese Acad Sci, Beijing 100049, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaChen, Jun论文数: 0 引用数: 0 h-index: 0机构: Zhejiang Univ, Coll Life Sci, Hangzhou 310058, Zhejiang, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaGuo, Taijie论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Ctr Excellence Mol Synth, Shanghai Inst Organ Chem, Key Lab Organofluorine Chem, 345 Ling Ling Rd, Shanghai 200032, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaMeng, Genyi论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Ctr Excellence Mol Synth, Shanghai Inst Organ Chem, Key Lab Organofluorine Chem, 345 Ling Ling Rd, Shanghai 200032, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaJiang, Biao论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaDong, Jiajia论文数: 0 引用数: 0 h-index: 0机构: Chinese Acad Sci, Ctr Excellence Mol Synth, Shanghai Inst Organ Chem, Key Lab Organofluorine Chem, 345 Ling Ling Rd, Shanghai 200032, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R ChinaLiu, Jia论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China ShanghaiTech Univ, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Shanghai Clin Res & Trial Ctr, Shanghai 201210, Peoples R China ShanghaiTech Univ, Gene Editing Ctr, Sch Life Sci & Technol, Shanghai 201210, Peoples R China Guangzhou Lab Guangzhou Int Bio Isl, 9 XingDaoHuanBei Rd, Guangzhou 510005, Guangdong, Peoples R China ShanghaiTech Univ, Shanghai Inst Adv Immunochem Studies, Shanghai 201210, Peoples R China
- [46] KPT330 improves Cas9 precision genome- and base-editing by selectively regulating mRNA nuclear exportCommunications Biology, 5Yan-ru Cui论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyShao-jie Wang论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyTiancheng Ma论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyPeihong Yu论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyJun Chen论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyTaijie Guo论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyGenyi Meng论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyBiao Jiang论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyJiajia Dong论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and TechnologyJia Liu论文数: 0 引用数: 0 h-index: 0机构: ShanghaiTech University,Shanghai Institute for Advanced Immunochemical Studies and School of Life Science and Technology
- [47] Correction of SCID-X1 by targeted genome editing of hematopoietic stem/progenitor cells (HSPC) in the mouse modelHUMAN GENE THERAPY, 2016, 27 (11) : A135 - A136Schiroli, G.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyGenovese, P.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyCapo, V.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyCastiello, M. C.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyAlbano, L.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalySanvito, F.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyHolmes, M. C.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci, Richmond, CA USA San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyVilla, A.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalySitia, G.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyLombardo, A.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, ItalyNaldini, L.论文数: 0 引用数: 0 h-index: 0机构: San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy San Raffaele Telethon Inst Gene Therapy SR Tiget, Milan, Italy
- [48] Author Correction: Engineering monocyte/macrophage−specific glucocerebrosidase expression in human hematopoietic stem cells using genome editingNature Communications, 11Samantha G. Scharenberg论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsEdina Poletto论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsKatherine L. Lucot论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsPasqualina Colella论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsAdam Sheikali论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsThomas J. Montine论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsMatthew H. Porteus论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of PediatricsNatalia Gomez-Ospina论文数: 0 引用数: 0 h-index: 0机构: Stanford University School of Medicine,Department of Pediatrics
- [49] Correction of SCID-X1 by Targeted Genome Editing of Hematopoietic Stem/Progenitor Cells (HSPC) in the Mouse ModelMOLECULAR THERAPY, 2016, 24 : S18 - S19Schiroli, Giulia论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy TIGET, Milan, ItalyGenovese, Pietro论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy TIGET, Milan, ItalyCapo, Valentina论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy TIGET, Milan, ItalyCastiello, Maria C.论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy TIGET, Milan, ItalyAlbano, Luisa论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy TIGET, Milan, ItalyHolmes, Michael C.论文数: 0 引用数: 0 h-index: 0机构: Sangamo BioSci, Richmond, CA USA TIGET, Milan, ItalyVilla, Anna论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy TIGET, Milan, ItalySitia, Giovanni论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, I-20132 Milan, Italy TIGET, Milan, ItalyLombardo, Angelo论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy TIGET, Milan, ItalyNaldini, Luigi论文数: 0 引用数: 0 h-index: 0机构: TIGET, Milan, Italy Univ Vita Salute San Raffaele, Milan, Italy TIGET, Milan, Italy
- [50] Reading Frame Correction by Targeted Genome Editing Restores Dystrophin Expression in Cells From Duchenne Muscular Dystrophy PatientsMOLECULAR THERAPY, 2013, 21 (09) : 1718 - 1726Ousterout, David G.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAPerez-Pinera, Pablo论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAThakore, Pratiksha I.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAKabadi, Ami M.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USABrown, Matthew T.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAQin, Xiaoxia论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Inst Genome Sci & Policy, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAFedrigo, Olivier论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Inst Genome Sci & Policy, Durham, NC 27708 USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA论文数: 引用数: h-index:机构:Tremblay, Jacques P.论文数: 0 引用数: 0 h-index: 0机构: Univ Laval, Fac Med, CHUQ, Unite Rech Genet Humaine,Ctr Rech CHUL, Quebec City, PQ G1K 7P4, Canada Duke Univ, Dept Biomed Engn, Durham, NC 27708 USAGersbach, Charles A.论文数: 0 引用数: 0 h-index: 0机构: Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA Duke Univ, Inst Genome Sci & Policy, Durham, NC 27708 USA Duke Univ, Med Ctr, Dept Orthopaed Surg, Durham, NC USA Duke Univ, Dept Biomed Engn, Durham, NC 27708 USA