An uplifted destiny for mucopolysaccharidosis type I with heart valve involvement

被引:0
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作者
Raffaele Manna
Francesca Graziani
Rosa Lillo
Elena Verrecchia
Luca Ludovico Sicignano
Donato Rigante
机构
[1] Fondazione Policlinico A. Gemelli IRCCS,Department of Internal Medicine
[2] Università Cattolica del Sacro Cuore,Department of Cardiovascular and Thoracic Sciences
[3] Fondazione Policlinico Universitario A. Gemelli IRCCS,Department of Life Sciences and Public Health
[4] Fondazione Policlinico Universitario A. Gemelli IRCCS,undefined
[5] Università Cattolica Sacro Cuore,undefined
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关键词
Mucopolysaccharidosis; Hurler–Scheie syndrome; Iduronidase; Heart valve replacement; Personalized medicine; Innovative biotechnologies; Lysosomal storage disorder;
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页码:2325 / 2326
页数:1
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