FDA approves first gene therapy for Duchenne muscular dystrophy, despite internal objections

被引：0
|
作者：
Asher Mullard
机构：
来源：
Nature Reviews Drug Discovery | 2023年 / 22卷
关键词：
D O I：
暂无
中图分类号：
学科分类号：
摘要：
引用
收藏
页码：610 / 610
相关论文
共 50 条
  • [21] Gene Therapy for Hemophilia and Duchenne Muscular Dystrophy in China
    Liu, Xionghao
    Liu, Mujun
    Wu, Lingqian
    Liang, Desheng
    HUMAN GENE THERAPY, 2018, 29 (02) : 146 - 150
  • [22] Gene therapy progress and prospects: Duchenne muscular dystrophy
    K Foster
    H Foster
    J G Dickson
    Gene Therapy, 2006, 13 : 1677 - 1685
  • [23] Personalized gene and cell therapy for Duchenne Muscular Dystrophy
    Barthelemy, Florian
    Wein, Nicolas
    NEUROMUSCULAR DISORDERS, 2018, 28 (10) : 803 - 824
  • [24] Progress in gene therapy for Duchenne muscular dystrophy.
    Clemens P.R.
    Duncan F.J.
    Current Neurology and Neuroscience Reports, 2001, 1 (1) : 89 - 96
  • [25] Progress toward Gene Therapy for Duchenne Muscular Dystrophy
    Chamberlain, Joel R.
    Chamberlain, Jeffrey S.
    MOLECULAR THERAPY, 2017, 25 (05) : 1125 - 1131
  • [26] Retroviral vectors for gene therapy of Duchenne muscular dystrophy
    Fassati, A
    Bresolin, N
    NEUROLOGICAL SCIENCES, 2000, 21 (05) : S925 - S927
  • [27] DWORF Gene Therapy for Duchenne Muscular Dystrophy Cardiomyopathy
    Morales, Emily
    Yue, Yongping
    Watkins, Thais
    Han, Jin
    Pan, Xiufang
    Gibson, Aaron
    Makarewich, Catherine
    Babu, Gopal
    Duan, Dongsheng
    MOLECULAR THERAPY, 2022, 30 (04) : 493 - 493
  • [28] Progress towards gene therapy for Duchenne muscular dystrophy
    Hauser, MA
    Chamberlain, JS
    JOURNAL OF ENDOCRINOLOGY, 1996, 149 (03) : 373 - 378
  • [29] Gene therapy progress and prospects: Duchenne muscular dystrophy
    Foster, K.
    Foster, H.
    Dickson, J. G.
    GENE THERAPY, 2006, 13 (24) : 1677 - 1685
  • [30] Retroviral vectors for gene therapy of Duchenne muscular dystrophy
    A. Fassati
    N. Bresolin
    Neurological Sciences, 2000, 21 : S925 - S927
12345